19 results on '"Duchenne muscular dystrophy (DMD)"'
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2. Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping (DELIVER)
3. Twice Weekly Steroids and Exercise as Therapy for DMD
4. A Study to Assess Safety/Tolerability, pk, Effects on Histology, Clinical Parameters of Givinostat in Children With DMD
5. A Study to Assess the Safety, Tolerability and Preliminary Efficacy of ASP0367 (MA-0211) in Pediatric Male Participants With Duchenne Muscular Dystrophy (DMD)
6. Peabody Developmental Motor Scaling In Children With Period Duchenne Muscular Dystrophy
7. Extension Study of NS-089/NCNP-02 in DMD
8. E-monitoring of PULMonary Function in Patients With Duchenne Muscular Dystrophy at Home" (E-PULMoDMD)
9. A Phase III Double-blind Study With Idebenone in Patients With Duchenne Muscular Dystrophy (DMD) Taking Glucocorticoid Steroids (SIDEROS)
10. A Low Interventional Study to Monitor Activity Using Wearable Sensors in Duchenne Muscular Dystrophy
11. Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular Dystrophy
12. Study of Eteplirsen in DMD Patients (PROMOVI)
13. Efficacy, Safety, and Tolerability Rollover Study of Eteplirsen in Subjects With Duchenne Muscular Dystrophy
14. To Compare the Pharmacokinetics Profiles of ISO 20, IBU 200 and IBU Plus ISO Combinations 200 + 20 (ISOFEN1)
15. Cardiomyopathy in DMD: Lisinopril vs. Losartan
16. Research of Biomarkers in Duchenne Muscular Dystrophy Patients (IBISD)
17. The Safety, Efficacy and Tolerability of Remote Ischemic Preconditioning as a Therapy to DMD
18. A Trial of Chronotherapy of Corticosteroids in Duchenne Muscular Dystrophy
19. Efficacy and Tolerability of Idebenone in Boys With Cardiac Dysfunction Associated With Duchenne Muscular Dystrophy (DELPHI)
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