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3. Gene editing without ex vivo culture evades genotoxicity in human hematopoietic stem cells

4. Therapeutic Gene Editing of HSCs Ex Vivo without in Vitro Culture Avoids Genotoxicity, Simplifies Procedures, and Preserves Efficiency and Stemness

5. Efficient Homology-Directed Repair with Circular Single-Stranded DNA Donors

6. Genome-wide detection of CRISPR editing in vivo using GUIDE-tag

7. Combined +58 and +55 BCL11A enhancer Editing Yields Exceptional Efficiency, Specificity and HbF Induction in Human and NHP Preclinical Models

8. Self-inactivating, all-in-one AAV vectors for precision Cas9 genome editing via homology-directed repair in vivo

13. Precision Cas9 Genome Editing in vivo with All-in-one, Self-targeting AAV Vectors

14. Efficient Homology-directed Repair with Circular ssDNA Donors

15. Enhanced Cas12a editing in mammalian cells and zebrafish

16. Majorana DUSEL R&D Final Report

17. Structure-guided chemical modification of guide RNA enables potent non-viral in vivo genome editing

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