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Start Over Topic anemia Publication Year Range This year Journal british journal of haematology
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1. Understanding complex disease‐related mechanisms: Rational therapies for Diamond–Blackfan anaemia.

Author

Lipton, Jeffrey M.

Subjects
*ANEMIA, *APLASTIC anemia, *ERYTHROCYTES, *ELTROMBOPAG, *HEMATOLOGY
Abstract

The rich history surrounding Diamond–Blackfan anaemia (DBA), originally described in 1938 as congenital hypoplastic anaemia2 reflects the evolution of paediatric haematology. In their paper, the authors1 present the results of a clinical trial using the thrombopoietin‐mimetic agent eltrombopag to treat red cell failure in DBA. A low response rate belies the importance of this work. Commentary on: Duncan et al. Treatment of refractory/relapsed Diamond–Blackfan anaemia with eltrombopag. Br J Haematol 2024;204:2077‐2085. [ABSTRACT FROM AUTHOR]

Published
2024
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