1. Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency
- Author
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Castiello, Maria Carmina, primary, Brandas, Chiara, additional, Ferrari, Samuele, additional, Porcellini, Simona, additional, Sacchetti, Nicolò, additional, Canarutto, Daniele, additional, Draghici, Elena, additional, Merelli, Ivan, additional, Barcella, Matteo, additional, Pelosi, Gabriele, additional, Vavassori, Valentina, additional, Varesi, Angelica, additional, Jacob, Aurelien, additional, Scala, Serena, additional, Basso Ricci, Luca, additional, Paulis, Marianna, additional, Strina, Dario, additional, Di Verniere, Martina, additional, Sergi Sergi, Lucia, additional, Serafini, Marta, additional, Holland, Steven M., additional, Bergerson, Jenna R. E., additional, De Ravin, Suk See, additional, Malech, Harry L., additional, Pala, Francesca, additional, Bosticardo, Marita, additional, Brombin, Chiara, additional, Cugnata, Federica, additional, Calzoni, Enrica, additional, Crooks, Gay M., additional, Notarangelo, Luigi D., additional, Genovese, Pietro, additional, Naldini, Luigi, additional, and Villa, Anna, additional
- Published
- 2024
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