189 results on '"Cheng, Seng"'
Search Results
2. Glucosylceramide synthase inhibition reduces ganglioside GM3 accumulation, alleviates amyloid neuropathology, and stabilizes remote contextual memory in a mouse model of Alzheimer’s disease
3. Adeno-associated viral vector serotype 9–based gene therapy for Niemann-Pick disease type A
4. A plain language summary of AAV-based gene therapy: challenges and potential solutions for people with antibodies against AAV
5. Rationale for using centralized transduction inhibition assays in three phase 3 rAAV gene therapy clinical trials
6. Realizing the promise of gene therapy through collaboration and partnering : Pfizer’s view
7. Liposome delivery systems
8. Molecular characterization of 'OsCURT1A' from upland rice in response to osmotic stress
9. Molecular characterisation of nerol dehydrogenase gene (PmNeDH) from Persicaria minor in response to stress-related phytohormones
10. Relicensing Practices of Taxi Drivers and Crane Operators Aged 70 Years and above in Singapore
11. Fetal gene therapy for neurodegenerative disease of infants
12. 'Benign' temporal lobe epilepsy with hippocampal sclerosis: A forgotten entity?
13. Glucosylceramide synthase inhibition alleviates aberrations in synucleinopathy models
14. Microarray dataset of transgenic rice overexpressing Abp57
15. Intravitreous injection of AAV2-sFLT01 in patients with advanced neovascular age-related macular degeneration: a phase 1, open-label trial
16. GENE THERAPY OF NEUROLOGICAL DISEASES
17. Rationally designed AAV2 and AAVrh8R capsids provide improved transduction in the retina and brain
18. Priapism in a Fabry disease mouse model is associated with upregulated penile nNOS and eNOS expression
19. Dysregulated DNA methylation in the pathogenesis of Fabry disease
20. Agarwood Induction: Current Developments and Future Perspectives
21. α-Galactosidase A Knockout Mice: Progressive Organ Pathology Resembles the Type 2 Later-Onset Phenotype of Fabry Disease
22. Glycosphingolipids are modulators of disease pathogenesis in amyotrophic lateral sclerosis
23. Additional file 5 of Glucosylceramide synthase inhibition reduces ganglioside GM3 accumulation, alleviates amyloid neuropathology, and stabilizes remote contextual memory in a mouse model of Alzheimer���s disease
24. Tetrahydrobiopterin deficiency in the pathogenesis of Fabry disease
25. Efficacy of Enzyme and Substrate Reduction Therapy with a Novel Antagonist of Glucosylceramide Synthase for Fabry Disease
26. AAV ‐mediated expression of galactose‐1‐phosphate uridyltransferase corrects defects of galactose metabolism in classic galactosemia patient fibroblasts
27. Molecular characterization of OsCURT1A from upland rice in response to osmotic stress
28. Gaucher-related synucleinopathies: The examination of sporadic neurodegeneration from a rare (disease) angle
29. “Benign” temporal lobe epilepsy with hippocampal sclerosis: A forgotten entity?
30. Nanometric material removal using electrokinetic phenomenon
31. Structural and kinetic studies of a novel nerol dehydrogenase from Persicaria minor, a nerol-specific enzyme for citral biosynthesis
32. Substrate reduction therapy using Genz‐667161 reduces levels of pathogenic components in a mouse model of neuronopathic forms of Gaucher disease
33. biAb Mediated Restoration of the Linkage between Dystroglycan and Laminin-211 as a Therapeutic Approach for α-Dystroglycanopathies
34. Microarray dataset of transgenic rice overexpressing Abp57
35. Crystallization and X-ray crystallographic analysis of recombinant TylP, a putative γ-butyrolactone receptor protein fromStreptomyces fradiae
36. Substrate reduction therapy using Genz‐667161 reduces levels of pathogenic components in a mouse model of neuronopathic forms of Gaucher disease.
37. Substrate Reduction Therapy for Sandhoff Disease through Inhibition of Glucosylceramide Synthase Activity
38. Agarwood Induction: Current Developments and Future Perspectives
39. Molecular characterisation of nerol dehydrogenase gene (PmNeDH) from Persicaria minor in response to stress-related phytohormones
40. Inhibiting neutral amino acid transport for the treatment of phenylketonuria
41. Universal Method for the Purification of Recombinant AAV Vectors of Differing Serotypes
42. Efficacy of Genz-682452-mediated inhibition of glucosylceramide synthase in a mouse model of Sandhoff disease
43. Priapism in a Fabry disease mouse model is associated with upregulated penile nNOS and eNOS expression
44. Structural and kinetic studies of a novel nerol dehydrogenase from Persicaria minor, a nerol-specific enzyme for citral biosynthesis
45. Microarray dataset of transgenic rice overexpressing Abp57
46. AB008. Bifunctional antibody as a surrogate molecular linker for the treatment of alpha-dystroglycan related muscular dystrophies
47. A randomised, double-blind, placebo-controlled trial of repeated nebulisation of non-viral cystic fibrosis transmembrane conductance regulator (CFTR) gene therapy in patients with cystic fibrosis
48. AAVS1-Targeted Plasmid Integration in AAV Producer Cell Lines
49. Characteristics of Minimally Oversized Adeno-Associated Virus Vectors Encoding Human Factor VIII Generated Using Producer Cell Lines and Triple Transfection
50. CRISPR/Cas9-Mediated Genome Editing as a Therapeutic Approach for Leber Congenital Amaurosis 10
Catalog
Books, media, physical & digital resources
Discovery Service for Jio Institute Digital Library
For full access to our library's resources, please sign in.