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Your search keyword '"de Castro, Maria Jose"' showing total 2 results
Start Over Author "de Castro, Maria Jose" Publisher academic press inc.
2 results on '"de Castro, Maria Jose"'

1. Interim results of Transpher A, a multicenter, single-dose, phase 1/2 clinical trial of ABO-102 gene therapy for Sanfilippo syndrome type A (mucopolysaccharidosis type IIIA).

Author

Flanigan, Kevin M., Smith, Nicholas J.C., Couce, Maria Luz, Truxal, Kristen V., McBride, Kim L., Simmons, Tabatha, de Castro, Maria Jose, Cope, Krista, Oreiro, Maria Teresa, Jaensch, Louise, Fuller, Maria, and Ruiz, Juan

Subjects
*GENE therapy, *SANFILIPPO syndrome, *CLINICAL trials, *HEPARAN sulfate, *INTRAVENOUS therapy
Published
2020
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2. Safety, tolerability and preliminary evidence of biopotency in Transpher B, a multicenter, single-dose, phase 1/2 clinical trial of ABO-101 gene therapy for Sanfilippo syndrome type B (mucopolysaccharidosis type IIIB).

Author

McBride, Kim L., Couce, Maria Luz, Flanigan, Kevin M., Truxal, Kristen V., Simmons, Tabatha, de Castro, Maria Jose, Rinaldi, Federica, Oreiro, Maria Teresa, Fuller, Maria, and Ruiz, Juan

Subjects
*GENE therapy, *SANFILIPPO syndrome, *CLINICAL trials, *HEPARAN sulfate, *INTRAVENOUS therapy
Published
2020
Full Text
View/download PDF

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