1. Rescue of a lysosomal storage disorder caused by Grn loss of function with a brain penetrant progranulin biologic
- Author
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Logan, Todd, primary, Simon, Matthew J., additional, Rana, Anil, additional, Cherf, Gerald M., additional, Srivastava, Ankita, additional, Davis, Sonnet S., additional, Yoon Low, Ray Lieh, additional, Chiu, Chi-Lu, additional, Fang, Meng, additional, Huang, Fen, additional, Bhalla, Akhil, additional, Llapashtica, Ceyda, additional, Prorok, Rachel, additional, Pizzo, Michelle E., additional, Calvert, Meredith E.K., additional, Sun, Elizabeth W., additional, Hsiao-Nakamoto, Jennifer, additional, Rajendra, Yashas, additional, Lexa, Katrina W., additional, Srivastava, Devendra B., additional, van Lengerich, Bettina, additional, Wang, Junhua, additional, Robles-Colmenares, Yaneth, additional, Kim, Do Jin, additional, Duque, Joseph, additional, Lenser, Melina, additional, Earr, Timothy K., additional, Nguyen, Hoang, additional, Chau, Roni, additional, Tsogtbaatar, Buyankhishig, additional, Ravi, Ritesh, additional, Skuja, Lukas L., additional, Solanoy, Hilda, additional, Rosen, Howard J., additional, Boeve, Bradley F., additional, Boxer, Adam L., additional, Heuer, Hilary W., additional, Dennis, Mark S., additional, Kariolis, Mihalis S., additional, Monroe, Kathryn M., additional, Przybyla, Laralynne, additional, Sanchez, Pascal E., additional, Meisner, Rene, additional, Diaz, Dolores, additional, Henne, Kirk R., additional, Watts, Ryan J., additional, Henry, Anastasia G., additional, Gunasekaran, Kannan, additional, Astarita, Giuseppe, additional, Suh, Jung H., additional, Lewcock, Joseph W., additional, DeVos, Sarah L., additional, and Di Paolo, Gilbert, additional
- Published
- 2024
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