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Your search keyword '"Szabo, S."' showing total 5 results
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5 results on '"Szabo, S."'

2. PRO63 THE NATURAL HISTORY OF DUCHENNE MUSCULAR DYSTROPHY IN THE CORTICOSTEROID ERA: A SYSTEMATIC REVIEW OF STUDIES FROM CANADA AND THE US.

Author

Deighton, A., Szabo, S., Salhany, R., Harwood, M., Mah, J., and Gooch, K.

Subjects
*DUCHENNE muscular dystrophy, *NATURAL history
Abstract

DMD is a severe progressive myopathy characterized by early loss of ambulation (LOA) and reduced life expectancy; and corticosteroids (CS) can delay disease progression. The objective was to summarize data on age at LOA and death from CS-treated patients with DMD. This analysis focused on studies with a minimum sample size >=50 CS-treated DMD patients from the US and Canada. [Extracted from the article]

Published
2019
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3. RW2 THE USE OF REAL-WORLD DATA IN HEALTH TECHNOLOGY ASSESSMENT OF MEDICATIONS FOR RARE DISEASES IN CANADA AND THE UK.

Author

Mickle, A., Harwood, M., Deighton, A., Qian, C., and Szabo, S.

Subjects
*RARE diseases, *MEDICAL technology, *TECHNOLOGY assessment, *DRUGS, *MEDICAL registries
Abstract

Data to characterize the burden of rare diseases, and the efficacy and safety of their treatment, are scarce. Health-services researchers and decision-makers are advocating for the consideration of real-world data (RWD) - data collected outside of randomized controlled trials - in health technology assessments (HTAs) of rare-disease medications. [Extracted from the article]

Published
2020
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