440 results on '"Balbir gurman, Alexandra"'
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2. Contributors
- Author
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Abu-Shakra, Mahmoud, primary, Adiguzel, Yekbun, additional, Al Shawaf, Maisam, additional, Alghory, Amal, additional, Almeida, Isabel, additional, Alrais, Mahmoud, additional, Alrifaai, Mohamad Aosama, additional, Alwani, Abdulkarim, additional, Alwani, Abdulrahman, additional, Amital, Howard, additional, Anna, Dubaniewicz, additional, Arleevskaya, Marina, additional, Ashkenazi, Shai, additional, Athanassiou, Lambros, additional, Athanassiou, Panagiotis, additional, Atik, Houda, additional, Atzeni, Fabiola, additional, Balbir-Gurman, Alexandra, additional, Balcioglu, Zeynep Betul, additional, Baldini, Chiara, additional, Barbour, Mohammad, additional, Bashi, Tomer, additional, Belyaeva, Irina V., additional, Ben-Ami, Dana, additional, Blank, Miri, additional, Boccassini, Laura, additional, Bogdanos, Dimitrios P., additional, Bombardieri, Stefano, additional, Bost, Chloé, additional, Brandão, Mariana, additional, Braun-Moscovici, Yolanda, additional, Brooks, Wesley H., additional, Campar, A., additional, Carvalheiras, Graziela, additional, Cervera, R., additional, Churilov, Leonid P., additional, Cohen, Eytan, additional, Correia, J., additional, Darkhabani, Mohammad, additional, David, Paula, additional, de Carvalho, Jozélio Freire, additional, Deniz, Omer Faruk, additional, Detrick, Barbara, additional, Deutsch, Melanie, additional, Di Battista, Marco, additional, Dogan, Emir, additional, Dogru, Omer Faruk, additional, Domingues, Vital Da Silva, additional, Dotan, Arad, additional, Dow, Coad Thomas, additional, Durai, Malarvizhi, additional, Elefante, Elena, additional, Elsalti, Abdulrahman, additional, Erman, Mikhail V., additional, Esirgun, Sevval Nil, additional, Ferrão, C., additional, Ferreira, Álvaro, additional, Ferro, Francesco, additional, Fonseca, Tomás, additional, Garg, Ravindra Kumar, additional, Guilherme, Luiza, additional, Habra, Mona, additional, Halpert, Gilad, additional, Hammerstad, Sara Salehi, additional, Hooks, John J., additional, Ilchovska, Daisy, additional, Invernizzi, Pietro, additional, Israeli, E., additional, Janket, Sok-Ja, additional, Kalil, Jorge, additional, Karaoglan, Birnur Sinem, additional, Kiyak, Zeynep, additional, Kol, Mustafa Yusuf, additional, Kostoglou-Athanassiou, Ifigenia, additional, Krause, Ilan, additional, Kudryavtsev, Igor V., additional, Kumar, Neeraj, additional, Lavine, Noy, additional, Lerman, Tsahi T., additional, Levi, Assi, additional, Ling, Eduard, additional, Moutsopoulos, Haralampos M., additional, Mahajna, Hussein, additional, Mahroum, Naim, additional, Malhotra, Hardeep Singh, additional, Malkova, Аnna M., additional, Maoz-Segal, Ramit, additional, Marinho, António, additional, Mavragani, Clio P., additional, Meurman, Jukka H., additional, Milhes, Jean, additional, Mimouni, Daniel, additional, Morais, Cátia Iracema, additional, Moudgil, Kamal D., additional, Muniz Caldas, Cezar Augusto, additional, Neves, Esmeralda, additional, Neyestani, Kamyar, additional, Nikolaev, Alexei V., additional, Noversa de Sousa, Rita, additional, Ohayon, Aviran, additional, Palumbo, Antonino, additional, Pasoto, Sandra Gofinet, additional, Petríková, Jana, additional, Puxeddu, Ilaria, additional, Raftopoulou, Sylvia, additional, Renaudineau, Yves, additional, Ribeiro, Francinne Machado, additional, Rigopoulou, Eirini I., additional, Rosário, Cristina, additional, Rossa, Alessandra Della, additional, Sahin, Meyha, additional, Sarzi-Puttini, Piercarlo, additional, Seguro, Luciana Parente Costa, additional, Seida, Isa, additional, Seida, Ravend, additional, Serpa Pinto, L., additional, Sharon, Eran, additional, Shoenfeld, Yehuda, additional, Smyk, Daniel S., additional, Sousa, Rita Catarina Medeiros, additional, Starshinova, Anna A., additional, Tamimi, Faleh, additional, Tocut, Milena, additional, Tomer, Yaron, additional, Tunitsky-Lifshitz, Yulia, additional, Vasconcelos, Carlos, additional, Vasconcelos, Júlia, additional, Vassilopoulos, Dimitrios, additional, Venkatesha, Shivaprasad H., additional, Villanueva, Ronald, additional, Vita, Pedro, additional, Yablonskiy, Piotr K., additional, Yilmaz, Mesut, additional, Zamorano, Bryan, additional, Zandman-Goddard, Gisele, additional, Zinchenko, Yulia S., additional, and Zoubi, Magdi, additional
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- 2024
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3. Infections and Systemic Sclerosis
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Balbir-Gurman, Alexandra, primary and Braun-Moscovici, Yolanda, additional
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- 2024
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4. Is cyclophosphamide still the gold standard in early severe rapidly progressive systemic sclerosis?
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Campochiaro, Corrado, Allanore, Yannick, Braun-Moscovici, Yolanda, Matucci-Cerinic, Marco, and Balbir-Gurman, Alexandra
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- 2024
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5. Does the Impact of COVID‐19 on Patients With Systemic Sclerosis Change Over Time?
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Deibel, Elisabeth, Carreira, Patricia E., Vonk, Madelon, del Papa, Nicoletta, Bečvář, Radim, Guillén‐Del‐Castillo, Alfredo, Campochiaro, Corrado, Poormoghim, Hadi, Liem, Sophie, Lazzaroni, Maria‐Grazia, Giollo, Alessandro, Mekinian, Arsène, de Vries‐Bouwstra, Jeska, De Santis, Maria, Balbir‐Gurman, Alexandra, Mihai, Carina, De Luca, Giacomo, Moiseev, Sergey, Zanatta, Elisabetta, Foti, Rosario, Rednic, Simona, Denton, Christopher, Cutolo, Maurizio, Belloli, Laura, Airo, Paolo, Garzanova, Liudmila, Moroncini, Gianluca, İnanç, Murat, Panopoulos, Stylianos, Tandaipan, Jose‐Luis, Chatelus, Emmanuel, Rosato, Edoardo, Kuwana, Masataka, Yavuz, Sule, Alegre‐Sancho, Juan J., Smith, Vanessa, Szűcs, Gabriella, Henes, Joerg, Rodríguez‐Pintó, Ignasi, Atzeni, Fabiola, Spierings, Julia, Truchetet, Marie‐Elise, Milchert, Marcin, Brito de Araujo, Daniel, Riemekasten, Gabriela, Bernardino, Vera, Martin, Thierry, del Galdo, Francesco, Vacca, Alessandra, Mendoza, Fabian, Midtvedt, Øyvind, Murdaca, Giuseppe, Santiago, Tânia, Codullo, Veronica, Cacciapaglia, Fabio, Walker, Ulrich, Brunborg, Cathrine, Tirelli, Francesca, Allanore, Yannick, Furst, Daniel E., Matucci, Marco, Gabrielli, Armando, Distler, Oliver, and Hoffmann‐Vold, Anna‐Maria
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- 2024
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6. Cohort Enrichment Strategies for Progressive Interstitial Lung Disease in Systemic Sclerosis From European Scleroderma Trials and Research
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Vacca, Alessandra, Giollo, Alessandro, Balbir-Gurman, Alexandra, Gheorghiu, Ana Maria, Marcoccia, Antonella, Herrick, Ariane, Radic, Mislav, Stamenkovic, Bojana, Anic, Branimir, Granel, Brigitte, Ribi, Camillo, Selmi, Carlo Francesco, Carlos de la Puente, Milano, de Souza Müller, Carolina, Denton, Christopher, Kayser, Cristiane, Tanaseanu, Cristina-Mihaela, Majewski, Dominik, Rimar, Doron, Krasowska, Dorota, Veale, Douglas, Walker, Ulrich, Kerzberg, Eduardo, Rezus, Elena, Zanatta, Elisabetta, Siegert, Elise, De Langhe, Ellen, Oksel, Fahrettin, Ingegnoli, Francesca, Cantatore, Francesco Paolo, Szücs, Gabriela, Cuomo, Giovanna, Seskute, Goda, Litinsky, VilniusIra, Castellví, Ivan, Morovic-Vergles, Jadranka, Sibilia, Jean, Henes, Jörg, Solanki, Kamal, Perdan-Pirkmajer, Katja, Herrmann, Kristine, Saketkoo, Lesley Ann, Stamp, Lisa, Mouthon, Luc, Salvador, Maria João, Pozzi, Maria Rosa, Üprus, Maria, Vanthuyne, Marie, Engelhart, Merete, Köhm, Michaela, Iudici, Michele, Inanc, Murat, Fathi, Nihal, Pamuk, Nuri, García de la Peña Lefebv, Paloma, Carreira, Patricia E., Bancel, Dominique Farge, Moroncini, Luca, Montecucco, C., Ancuta, Codrina, Sunderkötter, Cord, Müller-Ladner, Ulf, Rosato, Edoardo, Kucharz, Eugene J., Iannone, Florenzo, Del Galdo, Francesco, Poormoghim, Hadi, Kötter, Ina, Distler, Jörg, Cutolo, Maurizio, Tikly, Mohammed, Damjanov, Nemanja, Hunzelmann, Nicolas, Vlachoyiannopoulos, P., Hasler, Paul, Sarzi Puttini, Piercarlo, Wiland, Piotr, Becvar, Radim, Yavuz, Sule, Zdrojewski, Zbigniew, Pellerito, Raffaele, Foti, Rosario, Ionescu, Ruxandra Maria, Adler, Sabine, Kahl, Sarah, Moiseev, Sergey, Stebbings, Simon, Rednic, Simona, Negrini, Simone, Heitmann, Stefan, Ullman, Susanne, Agachi, Svetlana, Martin, Thierry, Schmeiser, Tim, Riccieri, Valeria, Smith, Vanessa, Bernardino, Vera, Ortiz-Santamaria, Vera, Hsu, Vivien M., Abdel Atty Mohamed, Walid Ahmed, Hoffmann-Vold, Anna-Maria, Brunborg, Cathrine, Airò, Paolo, Ananyeva, Lidia P., Czirják, László, Guiducci, Serena, Hachulla, Eric, Li, Mengtao, Mihai, Carina, Riemekasten, Gabriela, Sfikakis, Petros P., Valentini, Gabriele, Kowal-Bielecka, Otylia, Allanore, Yannick, and Distler, Oliver
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- 2023
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7. Stratification in systemic sclerosis according to autoantibody status versus skin involvement: a study of the prospective EUSTAR cohort
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Matucci Cerinic, Marco, Walker, Ulrich, Iannone, Florenzo, Jordan, Suzana, Becvar, Radim, Kowal Bielecka, Otylia, Cutolo, Maurizio, Cuomo, Giovanna, Kedor, Claudia, Rednic, Simona, Avouac, Jérome, Vlachoyiannopoulos, P., Montecucco, C., Stork, Jiri, Inanc, Murat, Carreira, Patricia E., Novak, Srdan, Czirják, László, Iudici, Michele, Kucharz, Eugene J., Zanatta, Elisabetta, Perdan-Pirkmajer, Katja, Coleiro, Bernard, Moroncini, Gianluca, Farge Bancel, Dominique, Airò, Paolo, Hesselstrand, Roger, Radic, Mislav, Braun-Moscovici, Yolanda, Lo Monaco, Andrea, Hunzelmann, Nicolas, Pellerito, Raffaele, Giollo, Alessandro, Morovic-Vergles, Jadranka, Denton, Christopher, Vonk, Madelon, Damjanov, Nemanja, Henes, Jörg, Ortiz Santamaria, Vera, Heitmann, Stefan, Krasowska, Dorota, Hasler, Paul, Kohm, Michaela, Foeldvari, Ivan, Bajocchi, Gianluigi, Salvador, Maria João, Stamenkovic, Bojana, Selmi, Carlo Francesco, Tikly, Mohammed, Ananieva, Lidia P., Herrick, Ariane, Müller-Ladner, Ulf, De Palma, Raffaele, Engelhart, Merete, Szücs, Gabriela, Sobrino Grande, Cristina, Midtvedt, Øyvind, Launay, David, Riccieri, Valeria, Ionescu, Ruxandra Maria, Sha, Ami, Gheorghiu, Ana Maria, Sunderkötter, Cord, Ingegnoli, Francesca, Mouthon, Luc, Smith, Vanessa, Cantatore, Francesco Paolo, Ullman, Susanne, Alberto von Mühlen, Carlos, Pozzi, Maria Rosa, Eyerich, Kilian, Wiland, Piotr, Vanthuyne, Marie, Alegre-Sancho, Juan Jose, Herrmann, Kristine, De Langhe, Ellen, Anic, Branimir, Üprus, Maria, Yavuz, Sule, Granel, Brigitte, de Souza Müller, Carolina, Busquets, Joanna, Agachi, Svetlana, Stebbings, Simon, Mathieu, D'Alessandro, Sampaio-Barros, Percival D., Stamp, Lisa, Solanki, Kamal, Veale, Douglas, Loyo, Esthela, Li, Mengtao, Abdel Atty Mohamed, Walid Ahmed, Gigante, Antonietta, Oksel, Fahrettin, Tanaseanu, Cristina-Mihaela, Foti, Rosario, Ancuta, Codrina, Maurer, Britta, van Laar, Jacob, Kayser, Cristiane, Fathi, Nihal, García de la Peña Lefebvre, Paloma, Sibilia, Jean, Litinsky, Ira, Abignano, Giuseppina, Seskute, Goda, Saketkoo, Lesley Ann, Kerzberg, Eduardo, Bianchi, Washington, Castellví, Ivan, Limonta, Massimiliano, Rimar, Doron, Couto, Maura, Spertini, François, Marcoccia, Antonella, Kahl, Sarah, Hsu, Ivien M., Martin, Thierry, Moiseev, Sergey, Chung, Lorinda S., Schmeiser, Tim, Majewski, Dominik, Zdrojewski, Zbigniew, Martínez-Barrio, Julia, Bernardino, Vera, Sommerlatte, Sabine, Levy, Yair, Rezus, Elena, Nuri Pamuk, Omer, Sarzi Puttini, Piercarlo, Poormoghim, Hadi, Kötter, Ina, Gaches, Francis, Belloli, Laura, Sfikakis, Petros, Markus, Juliana, Feldman, Gary R, Ramazan, Ana-Maria, Scherer, H.U., Truchetet, Marie-Elise, Lescoat, Alain, Dagna, Lorenzo, van Laar, J.M., Rudnicka, Lidia, Oliveira, Susana, Atzeni, Fabiola, Kuwana, Masataka, Mekinian, Arsene, Martin, Mickaël, Tanaka, Yoshiya, Elhai, Muriel, Sritharan, Nanthara, Boubaya, Marouane, Balbir-Gurman, Alexandra, Siegert, Elise, Hachulla, Eric, de Vries-Bouwstra, Jeska, Riemekasten, Gabriela, Distler, Jörg H W, Rosato, Edoardo, Del Galdo, Francesco, Mendoza, Fabian A, Furst, Daniel E, de la Puente, Carlos, Hoffmann-Vold, Anna-Maria, Gabrielli, Armando, Distler, Oliver, Bloch-Queyrat, Coralie, and Allanore, Yannick
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- 2022
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8. Environmental and societal factors associated with COVID-19-related death in people with rheumatic disease: an observational study
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Dahou, Brahim, Gómez, Gimena, Roberts, Karen, Baez, Roberto M, Castro Coello, Vanessa V, Haye Salinas, María J, Maldonado, Federico N, Reyes, Alvaro A, Alle, Gelsomina, Tanten, Romina, Maldonado Ficco, Hernán, Nieto, Romina, Gobbi, Carla, Tissera, Yohana, Pisoni, Cecilia, Paula, Alba, Albiero, Juan A, Schmid, Maria M, Cosatti, Micaela, Gamba, Maria J, Leandro, Carlevaris, Cusa, María A, German, Noelia, Bellomio, Veronica, Takashima, Lorena, Pera, Mariana, Cogo, Karina, Gálvez Elkin, Maria S, Medina, María A, Savio, Veronica, Rojas Tessel, Romina, Alamino, Rodolfo P, Werner, Marina L, Ornella, Sofía, Casalla, Luciana, de la Vega, Maria, Severina, María, García, Mercedes, Gonzalez Lucero, Luciana, Romeo, Cecilia, Moyano, Sebastián, Barbich, Tatiana, Bertoli, Ana, Baños, Andrea, Petruzzelli, Sandra, Matellan, Carla, Conti, Silvana, Lazaro, Maria A, Rodriguez Gil, Gustavo F, Risueño, Fabian, Quaglia, Maria I, Scafati, Julia, Cuchiaro, Natalia L, Rebak, Jonathan E, Pineda, Susana I, Calvo, María E, Picco, Eugenia, Yanzi, Josefina G, Maid, Pablo, Guaglianone, Debora, Morbiducci, Julieta S, Porta, Sabrina, Herscovich, Natalia, Velasco Zamora, José L, Kisluk, Boris, Castaños Menescardi, Maria S, Gallo, Rosana, Martire, María V, Maldini, Carla, Goizueta, Cecilia, de la Vega Fernandez, Sabrina S, Aeschlimann, Carolina, Subils, Gisela, Rath, Eva, Piette, Yves, Devinck, Mieke, Maeyaert, Bea, Machado Ribeiro, Francinne, Euzebio Ribeiro, Sandra L, Pinheiro, Marcelo, Ibáñez, Sebastián, Chassin Trubert, Anne-Marie, Dong, Lingli, Cajas, Lui, Barešić, Marko, Anić, Branimir, Ćulo, Melanie-Ivana, Pavelić, Tea A, Stranski, Kristina K, Karanovic, Boris, Vencovsky, Jiri, Píchová, Marta, Filkova, Maria, Hamoud, Hesham, Vassilopoulos, Dimitrios, Guzman Melgar, Gabriela M, So, Ho, Király, Márta, Vojdanian, Mahdi, Balbir Gurman, Alexandra, Abutiban, Fatemah, Zepa, Julija, Bulina, Inita, Bukauskiene, Loreta, Zazueta Montiel, Beatriz E, Castillo Ortiz, Angel A, Zamora Tehozol, Erick, Vega Morales, David, Cervántes Rosete, Diana, Martín Nares, Eduardo, Rodriguez Reyna, Tatiana S, Rull Gabayet, Marina, Alpízar Rodríguez, Deshiré, Irazoque, Fedra, Jimenez, Xochitl, Geurts van Bon, Lenny, Zijlstra, Theo, Hoekstra, Monique, Al Adhoubi, Nasra, Salim, Babur, Giraldo, Enrique, Salinas, Ariel, Ugarte Gil, Manuel, Nowakowski, Jarosław, Conway, Richard, Flood, Rachael, McCarthy, Geraldine, Felea, Ioana, Filipescu, Ileana, Rednic, Simona, Groseanu, Laura, Tamas, Maria M, Mlynarikova, Vanda, Skamlova, Martina, Zlnay, Martin, Mičeková, Dagmar, Capova, Lubica, Macejova, Zelmira, Šteňová, Emőke, Raffayova, Helena, Belakova, Gabriela, Strakova, Eva, Senčarová, Marieta, Žlnayová, Soňa, Sabová, Anna, Spisakova, Daniela, Oetterová, Mária, Lukacova, Olga, Bakosova, Martina, Hocevar, Alojzija, de la Torre Rubio, Natalia, Alegre Sancho, Juan J, Corteguera Coro, Montserrat, Cobeta Garcia, Juan C, Torres Martin, Maria C, Campos, Jose, Gomez Puerta, Jose A, Yardimci, Gozd K, Akar, Servet, Icacan, Ozan C, ÇELİK, Selda, Vasylets, Viktoriia, Yeoh, Su-Ann, Vandevelde, Claire, Dunt, Sasha, Leeder, Jane, Macphie, Elizabeth, Salerno, Rosaria, Graver, Christine, Williams, Katie, O'Reilly, Sheila, Devine, Kirsty, Tyler, Jennifer, Warner, Elizabeth, Pilcher, James, Patel, Samir, Nikiphorou, Elena, Chadwick, Laura, Jones, Caroline M, Harrison, Beverley, Thornton, Lucy, O'Kane, Diana, Fusi, Lucia, Low, Audrey, Horton, Sarah, Jatwani, Shraddha, Baig, Sara, Bajwa, Hammad, Berglund, Vernon, Dahle, Angela, Dorman, Walter, Hargrove, Jody, Hilton, Maren, Lebedoff, Nicholas, Leonard, Susan, Morgan, Jennifer, Pfeifer, Emily, Skemp, Archibald, Wilson, Jeffrey, Wolff, Anne, Cepeda, Eduardo, Todd, Derrick, Hare, Denise, Calabrese, Cassandra, Adams, Christopher, Khosroshahi, Arezou, Kilian, Adam, White, Douglas, Winter, Melanie, Fields, Theodore, Siegel, Caroline, Daver, Nicole, Harvey, Melissa, Kramer, Neil, Lamore, Concetta, Hogarty, Suneya, Yeter, Karen, Siddique, Faizah, Ban, Byung, Tanner, Tamar, Ruderman, Eric, Davis, William, Quinet, Robert, Scopelitis, Evangeline, Toribio, Karen, Webb Detiege, Tameka, Zakem, Jerald, Abbass, Khurram, Kepecs, Gilbert, Miranda, Lilliam, Guma, Michael, Haikal, Ammar, Mody, Sushama, Mueller, Daric, Jayatilleke, Arundathi, Zell, JoAnn, Bays, Alison, Dao, Kathryn, Ezzati, Fatemeh, Parks, Deborah, Karp, David, Quiceno, Guillermo, Izadi, Zara, Gianfrancesco, Milena A, Schmajuk, Gabriela, Jacobsohn, Lindsay, Katz, Patricia, Rush, Stephanie, Ja, Clairissa, Taylor, Tiffany, Shidara, Kie, Danila, Maria I, Wysham, Katherine D, Strangfeld, Anja, Mateus, Elsa F, Hyrich, Kimme L, Gossec, Laure, Carmona, Loreto, Lawson-Tovey, Saskia, Kearsley-Fleet, Lianne, Schaefer, Martin, Al-Emadi, Samar, Sparks, Jeffrey A, Hsu, Tiffany Y-T, Patel, Naomi J, Wise, Leanna, Gilbert, Emily, Duarte-García, Alí, Valenzuela-Almada, Maria O, Ugarte-Gil, Manuel F, Ljung, Lotta, Scirè, Carlo A, Carrara, Greta, Hachulla, Eric, Richez, Christophe, Cacoub, Patrice, Thomas, Thierry, Santos, Maria J, Bernardes, Miguel, Hasseli, Rebecca, Regierer, Anne, Schulze-Koops, Hendrik, Müller-Ladner, Ulf, Pons-Estel, Guillermo, Nieto, Romina E, Pisoni, Cecilia N, Tissera, Yohana S, Xavier, Ricardo, Lopes Marques, Claudia D, Pileggi, Gecilmara C S, Robinson, Philip C, Machado, Pedro M, Sirotich, Emily, Liew, Jean W, Hausmann, Jonathan S, Sufka, Paul, Grainger, Rebecca, Bhana, Suleman, Gore-Massy, Monique, Wallace, Zachary S, and Yazdany, Jinoos
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- 2022
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9. LGR5 expressing skin fibroblasts define a major cellular hub perturbed in scleroderma
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Gur, Chamutal, Wang, Shuang-Yin, Sheban, Fadi, Zada, Mor, Li, Baoguo, Kharouf, Fadi, Peleg, Hagit, Aamar, Suhail, Yalin, Adam, Kirschenbaum, Daniel, Braun-Moscovici, Yolanda, Jaitin, Diego Adhemar, meir-salame, Tomer, Hagai, Efrat, Kragesteen, Bjørt K., Avni, Batia, Grisariu, Sigal, Bornstein, Chamutal, Shlomi-Loubaton, Shir, David, Eyal, Shreberk-Hassidim, Rony, Molho-Pessach, Vered, Amar, Dalit, Tzur, Tomer, Kuint, Rottem, Gross, Moshe, Barboy, Oren, Moshe, Adi, Fellus-Alyagor, Liat, Hirsch, Dana, Addadi, Yoseph, Erenfeld, Shlomit, Biton, Moshe, Tzemach, Tehila, Elazary, Anat, Naparstek, Yaakov, Tzemach, Reut, Weiner, Assaf, Giladi, Amir, Balbir-Gurman, Alexandra, and Amit, Ido
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- 2022
- Full Text
- View/download PDF
10. Mood Problems and Depression in Systemic Sclerosis
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Balbir-Gurman, Alexandra, Braun-Moscovici, Yolanda, Matucci-Cerinic, Marco, editor, and Denton, Christopher P., editor
- Published
- 2021
- Full Text
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11. Outcomes of COVID-19 in patients with primary systemic vasculitis or polymyalgia rheumatica from the COVID-19 Global Rheumatology Alliance physician registry: a retrospective cohort study
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Dahou, Brahim, Rath, Eva, Piette, Yves, Devinck, Mieke, Maeyaert, Bea, Machado Ribeiro, Francinne, Euzebio Ribeiro, Sandra Lucia, Pinheiro, Marcelo, Quintana, Rosana, Gómez, Gimena, Roberts, Karen, Baez, Roberto Miguel, Castro Coello, Vanessa, Haye Salinas, María J., Maldonado, Federico Nicolas, Reyes Torres, Alvaro Andres, Alle, Gelsomina, Tanten, Romina, Maldonado Ficco, Hernán, Nieto, Romina, Gobbi, Carla, Tissera, Yohana, Pisoni, Cecilia, Paula, Alba, Albiero, Juan Alejandro, Schmid, Maria Marcela, Cosatti, Micaela, Gamba, Maria Julieta, Leandro, Carlevaris, Cusa, María Alejandra, German, Noelia, Bellomio, Veronica, Takashima, Lorena, Pera, Mariana, Cogo, Karina, Gálvez Elkin, Maria Soledad, Medina, María Alejandra, Savio, Veronica, Rojas Tessel, Ivana Romina, Perez Alamino, Rodolfo, Werner, Marina Laura, Ornella, Sofía, Casalla, Luciana, de la Vega, Maria, Severina, María, García, Mercedes, Gonzalez Lucero, Luciana, Romeo, Cecilia, Moyano, Sebastián, Barbich, Tatiana, Bertoli, Ana, Baños, Andrea, Petruzzelli, Sandra, Matellan, Carla, Conti, Silvana, Lazaro, Ma. Alicia, Rodriguez Gil, Gustavo Fabián, Risueño, Fabian, Quaglia, Maria Isabel, Scafati, Julia, Cuchiaro, Natalia Lili, Rebak, Jonathan Eliseo, Pineda, Susana Isabel, Calvo, María Elena, Picco, Eugenia, Gallino Yanzi, Josefina, Maid, Pablo, Guaglianone, Debora, Morbiducci, Julieta Silvana, Porta, Sabrina, Herscovich, Natalia, Velasco Zamora, José Luis, Kisluk, Boris, Castaños Menescardi, Maria Sol, Gallo, Rosana, Martire, María Victoria, Maldini, Carla, Goizueta, Cecilia, de la Vega Fernandez, Sabrina Solange, Aeschlimann, Carolina, Subils, Gisela, Ibáñez, Sebastián, Chassin-Trubert, Anne-Marie, Dong, Lingli, Cajas, Lui, Barešic, Marko, Anic, Branimir, Culo, Melanie-Ivana, Pavelic, Tea Ahel, Kovacevic Stranski, Kristina, Karanovic, Boris, Vencovsky, Jiri, Píchová, Marta, Filkova, Maria, Hamoud, Hesham, Vassilopoulos, Dimitrios, Guzman Melgar, Gabriela Maria, So, Ho, Király, Márta, Vojdanian, Mahdi, Balbir-Gurman, Alexandra, Abutiban, Fatemah, Zepa, Julija, Bulina, Inita, Bukauskiene, Loreta, Zaueta, Beatriz, Castillo Ortiz, Angel Alejandro, Zamora Tehozol, Erick, Vega, David, Cervántes Rosete, Diana, Martín Nares, Eduardo, Rodriguez-Reyna, Tatiana Sofia, Rull Gabayet, Marina, Alpízar-Rodríguez, Deshiré, Irazoque, Fedra, Jimenez, Xochitl, Geurts-van Bon, Lenny, Zijlstra, Theo, Hoekstra, Monique, Al-Adhoubi, Nasra, Salim, Babur, Giraldo, Enrique, Salinas, Ariel, Ugarte-Gil, Manuel, Nowakowski, Jaroslaw, Al-Emadi, Samar, Conway, Richard, Flood, Rachael, McCarthy, Geraldine, Felea, Ioana, Filipescu, Ileana, Rednic, Simona, Groseanu, Laura, Tamas, Maria Magdelena, Mlynarikova, Vanda, Skamlova, Martina, Zlnay, Martin, Miceková, Dagmar, Capova, Lubica, Macejova, Zelmira, Štenová, Emoke, Raffayova, Helena, Belakova, Gabriela, Strakova, Eva, Sencarová, Marieta, Žlnayová, Sona, Anna Sabová, Anna, Spisakova, Daniela, Oetterová, Mária, Lukacova, Olga, Bakosova, Martina, Hocevar, Alojzija, de la Torre-Rubio, Natalia, Alegre Sancho, Juan José, Corteguera Coro, Montserrat, Cobeta Garcia, Juan Carlos, Torres Martin, Maria Carmen, Campos, Jose, Gomez Puerta, Jose A, Yardimci, Gozd Kubra, Akar, Servet, Icacan, Ozan Cemal, Çelik, Selda, Vasylets, Viktoriia, Yeoh, Su-Ann, Vandevelde, Claire, Dunt, Sasha, Leeder, Jane, Macphie, Elizabeth, Salerno, Rosaria, Graver, Christine, Williams, Katie, O'Reilly, Sheila, Devine, Kirsty, Tyler, Jennifer, Warner, Elizabeth, Pilcher, James, Patel, Samir, Nikiphorou, Elena, Chadwick, Laura, Jones, Caroline Mulvaney, Harrison, Beverley, Thornton, Lucy, O'Kane, Diana, Fusi, Lucia, Low, Audrey, Horton, Sarah, Jatwani, Shraddha, Baig, Sara, Bajwa, Hammad, Berglund, Vernon, Dahle, Angela, Dorman, Walter, Hargrove, Jody, Hilton, Maren, Lebedoff, Nicholas, Leonard, Susan, Morgan, Jennifer, Pfeifer, Emily, Skemp, Archibald, Wilson, Jeffrey, Wolff, Anne, Cepeda, Eduardo, D'Silva, Kristin, Hsu, Tiffany, Patel, Naomi, Sparks, Jeffrey, Todd, Derrick, Wallace, Zachary, Hare, Denise, Calabrese, Cassandra, Adams, Christopher, Khosroshahi, Arezou, Kilian, Adam, White, Douglas, Winter, Melanie, Fields, Theodore, Siegel, Caroline, Daver, Nicole, Harvey, Melissa, Kramer, Neil, Lamore, Concetta, Hogarty, Suneya, Yeter, Karen, Wise, Leanna, Siddique, Faizah, Ban, Byung, Tanner, Tamar, Ruderman, Eric, Davis, William, Quinet, Robert, Scopelitis, Evangeline, Toribio Toribio, Karen, Webb-Detiege, Tameka, Zakem, Jerald, Abbass, Khurram, Kepecs, Gilbert, Miranda, Lilliam, Guma, Michael, Haikal, Ammar, Mody, Sushama, Mueller, Daric, Jayatilleke, Arundathi, Zell, JoAnn, Bays, Alison, Dao, Kathryn, Fatemeh, Ezzati, Parks, Deborah, Karp, David, Quiceno, Guillermo, Sattui, Sebastian E, Putman, Michael S, Seet, Andrea M, Gianfrancesco, Milena A, Beins, Kaley, Hill, Catherine, Liew, David, Mackie, Sarah L, Mehta, Puja, Neill, Lorna, Gomez, Gimena, Salinas, Maria Isabel Haye, Mariz, Henrique Ataide, de Sousa Studart, Samia Araujo, Araujo, Nafice Costa, Knight, Ann, Rozza, Davide, Quartuccio, Luca, Samson, Maxime, Bally, Stéphane, Maria, Alexandre TJ, Chazerain, Pascal, Hasseli, Rebecca, Müller-Ladner, Ulf, Hoyer, Bimba F, Voll, Reinhard, Torres, Rita Pinheiro, Luis, Mariana, Ribeirio, Sandra Lucia Euzebio, Sparks, Jeffrey A, Hsu, Tiffany Y-T, D’Silva, Kristin M, Patel, Naomi J, Gilbert, Emily, Almada, Maria Valenzuela, Duarte-García, Alí, Jacobsohn, Lindsay, Izadi, Zara, Strangfeld, Anja, Mateus, Elsa F, Hyrich, Kimme L, Gossec, Laure, Carmona, Loreto, Lawson-Tovey, Saskia, Kearsley-Fleet, Lianne, Schaefer, Martin, Sirotich, Emily, Hausmann, Jonathan S, Sufka, Paul, Bhana, Suleman, Liew, Jean W, Grainger, Rebecca, Machado, Pedro M, Wallace, Zachary S, Yazdany, Jinoos, and Robinson, Philip C
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- 2021
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12. Peripheral B cells repress B-cell regeneration in aging through a TNF-α/IGFBP-1/IGF-1 immune-endocrine axis
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Dowery, Reem, Benhamou, David, Benchetrit, Eli, Harel, Ofer, Nevelsky, Alex, Zisman-Rozen, Simona, Braun-Moscovici, Yolanda, Balbir-Gurman, Alexandra, Avivi, Irit, Shechter, Arik, Berdnik, Daniela, Wyss-Coray, Tony, and Melamed, Doron
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- 2021
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13. The Association Between Serum Ferritin Levels and Main Systemic Sclerosis Features: A Retrospective Study from a Tertiary Center.
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Markovich Sholomon, Shirley, Giryes, Sami, Shataylo, Vika, Braun-Moscovici, Yolanda, and Balbir-Gurman, Alexandra
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- 2024
14. IgG4-related Breast Disease: Review of the Literature.
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Jeries, Helana, Braun-Moscovici, Yolanda, and Balbir-Gurman, Alexandra
- Subjects
LACRIMAL apparatus ,RETROPERITONEUM ,SALIVARY glands ,COMPUTED tomography - Abstract
IgG4-related disease (IgG4-RD) is a rare illness with inflammatory and fibrotic changes in affected organs such as pancreas, thyroid, salivary or lacrimal glands, and retroperitoneal space; rarely other organs may be involved. IgG4-related breast disease (IgG4-BD) is very rare and generally presents as a lump or mastitis. IgG4-BD as a presenting feature of IgG4-RD is extremely rare. Hence, this paper reviews the known (n=48) IgG-BD cases reported in the literature to date. The majority of cases were diagnosed on routine mammography or during assessment for other clinically significant features. The absence of a lump border, and especially the absence of calcifications on ultrasonography, mammography, or computed tomography, is typical for IgG4-BD. Characteristic IgG4-BD pathological findings were dense lymphoplasmacytic infiltration with stromal fibrosis, and more than 10% IgG4
+ plasma cells/high-power field (HPF); the mean percentage of IgG4+ /IgG+ plasma cells was 54.2%, and only one-third of the patients had all "classical" signs of IgG4-BD including storiform fibrosis and obliterative phlebitis. Most of the cases had a benign course and responded to surgical excision with or without steroid therapy. [ABSTRACT FROM AUTHOR]- Published
- 2024
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15. Untangling the relationship between smoking and systemic sclerosis: an analysis of the EUSTAR cohort
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Ciaffi, Jacopo, primary, Liem, Sophie I E, additional, Cannegieter, Suzanne, additional, Ahmed, Saad, additional, Hoekstra, Eva M, additional, Wiland, Piotr, additional, Atsumi, Tatsuya, additional, Szücs, Gabriella, additional, Balbir Gurman, Alexandra, additional, Czirják, László, additional, Zanatta, Elisabetta, additional, Koetter, Ina, additional, Henes, Joerg C, additional, Matucci-Cerinic, Marco, additional, Airò, Paolo, additional, Ursini, Francesco, additional, Huizinga, Tom W J, additional, De Vries-Bouwstra, Jeska, additional, and Collaborators, EUSTAR, additional
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- 2024
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16. Outcomes of limited cutaneous systemic sclerosis patients: Results on more than 12,000 patients from the EUSTAR database
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Frantz, Camelia, Huscher, Dorte, Avouac, Jérôme, Hachulla, Eric, Balbir-Gurman, Alexandra, Riemekasten, Gabriela, Siegert, Elise, Lazzaroni, Maria-Grazia, Carreira, Patricia E., Vettori, Serena, Zanatta, Elisabetta, Ullman, Susanne, Czirjàk, Laszlo, Kowal-Bielecka, Otylia, Distler, Oliver, Matucci-Cerinic, Marco, and Allanore, Yannick
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- 2020
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17. EULAR recommendations for the treatment of systemic sclerosis: 2023 update
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Del Galdo, Francesco; https://orcid.org/0000-0002-8528-2283, Lescoat, Alain; https://orcid.org/0000-0003-2081-8558, Conaghan, Philip G; https://orcid.org/0000-0002-3478-5665, Bertoldo, Eugenia, Čolić, Jelena, Santiago, Tânia; https://orcid.org/0000-0002-1562-4022, Suliman, Yossra Atef; https://orcid.org/0000-0003-2919-1966, Matucci-Cerinic, Marco; https://orcid.org/0000-0002-9324-3161, Gabrielli, Armando, Distler, Oliver; https://orcid.org/0000-0002-0546-8310, Hoffmann-Vold, Anna-Maria; https://orcid.org/0000-0001-6467-7422, Castellví, Ivan; https://orcid.org/0000-0002-5410-5807, Balbir-Gurman, Alexandra, Vonk, Madelon; https://orcid.org/0000-0002-2266-9907, Ananyeva, Lidia, Rednic, Simona, Tarasova, Anna, Ostojic, Pedrag, Boyadzhieva, Vladimira, El Aoufy, Khadija, Farrington, Sue, Galetti, Ilaria, Denton, Christopher P; https://orcid.org/0000-0003-3975-8938, Kowal-Bielecka, Otylia, Mueller-Ladner, Ulf, Allanore, Yannick; https://orcid.org/0000-0002-6149-0002, Del Galdo, Francesco; https://orcid.org/0000-0002-8528-2283, Lescoat, Alain; https://orcid.org/0000-0003-2081-8558, Conaghan, Philip G; https://orcid.org/0000-0002-3478-5665, Bertoldo, Eugenia, Čolić, Jelena, Santiago, Tânia; https://orcid.org/0000-0002-1562-4022, Suliman, Yossra Atef; https://orcid.org/0000-0003-2919-1966, Matucci-Cerinic, Marco; https://orcid.org/0000-0002-9324-3161, Gabrielli, Armando, Distler, Oliver; https://orcid.org/0000-0002-0546-8310, Hoffmann-Vold, Anna-Maria; https://orcid.org/0000-0001-6467-7422, Castellví, Ivan; https://orcid.org/0000-0002-5410-5807, Balbir-Gurman, Alexandra, Vonk, Madelon; https://orcid.org/0000-0002-2266-9907, Ananyeva, Lidia, Rednic, Simona, Tarasova, Anna, Ostojic, Pedrag, Boyadzhieva, Vladimira, El Aoufy, Khadija, Farrington, Sue, Galetti, Ilaria, Denton, Christopher P; https://orcid.org/0000-0003-3975-8938, Kowal-Bielecka, Otylia, Mueller-Ladner, Ulf, and Allanore, Yannick; https://orcid.org/0000-0002-6149-0002
- Abstract
OBJECTIVES: To update the 2017 European Alliance of Associations for Rheumatology (EULAR) recommendations for treatment of systemic sclerosis (SSc), incorporating new evidence and therapies. METHODS: An international task force was convened in line with EULAR standard operating procedures. A nominal group technique exercise was performed in two rounds to define questions underpinning a subsequent systematic literature review. The evidence derived was discussed and overarching principles, recommendations and future research agenda were iteratively developed with voting rounds. RESULTS: The task force agreed on 22 recommendations covering 8 clinical/organ domains including Raynaud's phenomenon, digital ulcers, pulmonary arterial hypertension, scleroderma renal crisis, skin fibrosis, interstitial lung disease (ILD), gastrointestinal manifestations and arthritis. Most new recommendations are related to skin fibrosis and ILD. These included novel recommendations for the use of mycophenolate mofetil, nintedanib, rituximab and tocilizumab for the treatment of these crucial disease manifestations. The recommendations also included first-line and second-line interventions, providing increased utility for rheumatology practitioners. Important additions to the future research agenda included consideration of novel interventions for the management of vascular, musculoskeletal and gastrointestinal manifestations and calcinosis, as well as for the local management of digital ulcers. CONCLUSION: These updated recommendations include the first set of synthetic and biological targeted therapies recommended for key fibrotic manifestations of SSc as well as first-line combination treatment for newly diagnosed pulmonary artery hypertension and prioritise a new research agenda for the coming years.
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- 2024
18. Does the impact of COVID-19 on patients with systemic sclerosis change over time?
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Deibel, Elisabeth; https://orcid.org/0000-0003-4652-9826, Carreira, Patricia E, Vonk, Madelon; https://orcid.org/0000-0002-2266-9907, Del Papa, Nicoletta; https://orcid.org/0000-0003-1549-8852, Bečvář, Radim, Guillén-Del-Castillo, Alfredo, Campochiaro, Corrado; https://orcid.org/0000-0001-6806-3794, Poormoghim, Hadi, Liem, Sophie; https://orcid.org/0000-0003-0328-7062, Lazzaroni, Maria-Grazia, Giollo, Alessandro, Mekinian, Arsène; https://orcid.org/0000-0003-2849-3049, de Vries-Bouwstra, Jeska, De Santis, Maria; https://orcid.org/0000-0002-3196-1336, Balbir-Gurman, Alexandra, Mihai, Carina; https://orcid.org/0000-0002-8627-8817, De Luca, Giacomo; https://orcid.org/0000-0002-5306-7714, Moiseev, Sergey, Zanatta, Elisabetta, Foti, Rosario, Rednic, Simona, Denton, Christopher; https://orcid.org/0000-0003-3975-8938, Cutolo, Maurizio; https://orcid.org/0000-0002-5396-0932, Belloli, Laura, Airo, Paolo, Garzanova, Liudmila, Moroncini, Gianluca, Tirelli, Francesca, Distler, Oliver; https://orcid.org/0000-0002-0546-8310, Hoffmann-Vold, Anna-Maria; https://orcid.org/0000-0001-6467-7422, et al, Deibel, Elisabeth; https://orcid.org/0000-0003-4652-9826, Carreira, Patricia E, Vonk, Madelon; https://orcid.org/0000-0002-2266-9907, Del Papa, Nicoletta; https://orcid.org/0000-0003-1549-8852, Bečvář, Radim, Guillén-Del-Castillo, Alfredo, Campochiaro, Corrado; https://orcid.org/0000-0001-6806-3794, Poormoghim, Hadi, Liem, Sophie; https://orcid.org/0000-0003-0328-7062, Lazzaroni, Maria-Grazia, Giollo, Alessandro, Mekinian, Arsène; https://orcid.org/0000-0003-2849-3049, de Vries-Bouwstra, Jeska, De Santis, Maria; https://orcid.org/0000-0002-3196-1336, Balbir-Gurman, Alexandra, Mihai, Carina; https://orcid.org/0000-0002-8627-8817, De Luca, Giacomo; https://orcid.org/0000-0002-5306-7714, Moiseev, Sergey, Zanatta, Elisabetta, Foti, Rosario, Rednic, Simona, Denton, Christopher; https://orcid.org/0000-0003-3975-8938, Cutolo, Maurizio; https://orcid.org/0000-0002-5396-0932, Belloli, Laura, Airo, Paolo, Garzanova, Liudmila, Moroncini, Gianluca, Tirelli, Francesca, Distler, Oliver; https://orcid.org/0000-0002-0546-8310, Hoffmann-Vold, Anna-Maria; https://orcid.org/0000-0001-6467-7422, and et al
- Abstract
OBJECTIVE Outcome of COVID-19 patients improved over the pandemic, including patients with systemic rheumatic diseases. However, data on systemic sclerosis (SSc) patients are lacking. This study aimed to assess the outcome of SSc patients with COVID-19 over several waves. METHODS SSc patients with COVID-19 registered in the European Scleroderma Trials and Research group (EUSTAR) were collected between April 2020 and April 2021. Patients were assigned to wave 1 to 3 depending on date of COVID-19. Primary endpoints were death, intensive care unit stay or ventilatory support (severe outcome). Subgroup analyses of patients who were hospitalized or died were conducted. General and SSc-specific characteristics and treatment were compared over the waves. Descriptive statistics and multivariate logistic regression were applied. RESULTS 333 patients were included; 57 patients (17%) had a severe outcome, and 30 patients died (9%). Compared to wave 1, significantly fewer SSc patients suffered from severe COVID-19 in wave 2 and 3 (28.2% vs. 9.8% and 12.7%; p<0.001), less patients required hospitalization (46.7% vs. 19.6% and 25.5%; p<0.001) or ventilatory support (24.0% vs. 8.7% and 10.9%; p=0.001) and fewer patients died (15.7% vs. 5.0% and 7.5%; p=0.011). Patients were significantly younger, more often male, had less frequently arterial hypertension and less SSc cardiac involvement over wave 1 to 3. Patients received significantly less medium to high dose corticosteroids as SSc treatment. CONCLUSIONS Outcome of SSc patients with COVID-19 improved significantly over time, due to intrinsic and extrinsic factors. This article is protected by copyright. All rights reserved.
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- 2024
19. Does the impact of COVID-19 on patients with systemic sclerosis change over time?
- Author
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MS Reumatologie/Immunologie/Infectie, Infection & Immunity, Deibel, Elisabeth, Carreira, Patricia E, Vonk, Madelon, Del Papa, Nicoletta, Bečvář, Radim, Guillén-Del-Castillo, Alfredo, Campochiaro, Corrado, Poormoghim, Hadi, Liem, Sophie, Lazzaroni, Maria-Grazia, Giollo, Alessandro, Mekinian, Arsène, de Vries-Bouwstra, Jeska, De Santis, Maria, Balbir-Gurman, Alexandra, Mihai, Carina, De Luca, Giacomo, Moiseev, Sergey, Zanatta, Elisabetta, Foti, Rosario, Rednic, Simona, Denton, Christopher, Cutolo, Maurizio, Belloli, Laura, Airo, Paolo, Garzanova, Liudmila, Moroncini, Gianluca, İnanç, Murat, Panopoulos, Stylianos, Tandaipan, Jose-Luis, Chatelus, Emmanuel, Rosato, Edoardo, Kuwana, Masataka, Yavuz, Sule, Alegre-Sancho, Juan J, Smith, Vanessa, Szűcs, Gabriella, Henes, Joerg, Rodríguez-Pintó, Ignasi, Atzeni, Fabiola, Spierings, Julia, Truchetet, Marie-Elise, Milchert, Marcin, Brito de Araujo, Daniel, Riemekasten, Gabriela, Bernardino, Vera, Martin, Thierry, Del Galdo, Francesco, Vacca, Alessandra, Mendoza, Fabian, Midtvedt, Øyvind, Murdaca, Giuseppe, Santiago, Tânia, Codullo, Veronica, Cacciapaglia, Fabio, Walker, Ulrich, Brunborg, Cathrine, Tirelli, Francesca, Allanore, Yannick, Furst, Daniel E, Matucci, Marco, Gabrielli, Armando, Distler, Oliver, Hoffmann-Vold, Anna-Maria, MS Reumatologie/Immunologie/Infectie, Infection & Immunity, Deibel, Elisabeth, Carreira, Patricia E, Vonk, Madelon, Del Papa, Nicoletta, Bečvář, Radim, Guillén-Del-Castillo, Alfredo, Campochiaro, Corrado, Poormoghim, Hadi, Liem, Sophie, Lazzaroni, Maria-Grazia, Giollo, Alessandro, Mekinian, Arsène, de Vries-Bouwstra, Jeska, De Santis, Maria, Balbir-Gurman, Alexandra, Mihai, Carina, De Luca, Giacomo, Moiseev, Sergey, Zanatta, Elisabetta, Foti, Rosario, Rednic, Simona, Denton, Christopher, Cutolo, Maurizio, Belloli, Laura, Airo, Paolo, Garzanova, Liudmila, Moroncini, Gianluca, İnanç, Murat, Panopoulos, Stylianos, Tandaipan, Jose-Luis, Chatelus, Emmanuel, Rosato, Edoardo, Kuwana, Masataka, Yavuz, Sule, Alegre-Sancho, Juan J, Smith, Vanessa, Szűcs, Gabriella, Henes, Joerg, Rodríguez-Pintó, Ignasi, Atzeni, Fabiola, Spierings, Julia, Truchetet, Marie-Elise, Milchert, Marcin, Brito de Araujo, Daniel, Riemekasten, Gabriela, Bernardino, Vera, Martin, Thierry, Del Galdo, Francesco, Vacca, Alessandra, Mendoza, Fabian, Midtvedt, Øyvind, Murdaca, Giuseppe, Santiago, Tânia, Codullo, Veronica, Cacciapaglia, Fabio, Walker, Ulrich, Brunborg, Cathrine, Tirelli, Francesca, Allanore, Yannick, Furst, Daniel E, Matucci, Marco, Gabrielli, Armando, Distler, Oliver, and Hoffmann-Vold, Anna-Maria
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- 2024
20. Microangiopathy and forearm arterial blood flow in systemic sclerosis: a controlled study
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Bieber, Amir, Dolnikov, Katya, Chizik, Victoria, Novofastovsky, Irina, Fawaz, Abdallah, Balbir-Gurman, Alexandra, and Mader, Reuven
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- 2020
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21. Mood Problems and Depression in Systemic Sclerosis
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Balbir-Gurman, Alexandra, primary and Braun-Moscovici, Yolanda, additional
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- 2020
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22. Imaging aspects of interstitial lung disease in patients with rheumatoid arthritis: Literature review
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Balbir-Gurman, Alexandra, Guralnik, Ludmila, Yigla, Mordechai, Braun-Moscovici, Yolanda, and Hardak, Emilia
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- 2018
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23. IgA vasculitis in adults, pediatrics and non-vasculitic IgA nephropathy, retrospective analysis from 2 centers
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Levanon, Shirel, primary, Gotloib, Vera, additional, Kraus, Yehudit, additional, Novofastovski, Irina, additional, Brikman, Shay, additional, Fawaz, Abdallah, additional, Egbaria, Mohammad, additional, Butbul Aviel, Yonatan, additional, Balbir-Gurman, Alexandra, additional, Mader, Reuven, additional, and Bieber, Amir, additional
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- 2023
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24. Comparison of risk stratification models for prediction of mortality in SSc-PAH in EUSTAR
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Bjørkekjær, Hilde Jenssen, primary, Bruni, Cosimo, additional, Carreira, Patricia, additional, Airò, Paolo, additional, Simeón-Aznar, Carmen Pilar, additional, Truchetet, Marie-Elise, additional, Giollo, Alessandro, additional, Balbir-Gurman, Alexandra, additional, Martin, Mickael, additional, Denton, Christopher P, additional, Gabrielli, Armando, additional, Fretheim, Håvard, additional, Barua, Imon, additional, Bitter, Helle, additional, Midtvedt, Øyvind, additional, Garen, Torhild, additional, Broch, Kaspar, additional, Andreassen, Arne, additional, Tanaka, Yoshiya, additional, Riemekasten, Gabriela, additional, Müller-Ladner, Ulf, additional, Matucci-Cerinic, Marco, additional, Castellví, Ivan, additional, Siegert, Elise, additional, Hachulla, Eric, additional, Distler, Oliver, additional, and Hoffmann-Vold, Anna-Maria, additional
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- 2023
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25. Does the impact of COVID‐19 on patients with systemic sclerosis change over time?
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Deibel, Elisabeth, primary, Carreira, Patricia E., additional, Vonk, Madelon, additional, del Papa, Nicoletta, additional, Bečvář, Radim, additional, Guillén‐Del‐Castillo, Alfredo, additional, Campochiaro, Corrado, additional, Poormoghim, Hadi, additional, Liem, Sophie, additional, Lazzaroni, Maria‐Grazia, additional, Giollo, Alessandro, additional, Mekinian, Arsène, additional, de Vries‐Bouwstra, Jeska, additional, De Santis, Maria, additional, Balbir‐Gurman, Alexandra, additional, Mihai, Carina, additional, De Luca, Giacomo, additional, Moiseev, Sergey, additional, Zanatta, Elisabetta, additional, Foti, Rosario, additional, Rednic, Simona, additional, Denton, Christopher, additional, Cutolo, Maurizio, additional, Belloli, Laura, additional, Airo, Paolo, additional, Garzanova, Liudmila, additional, Moroncini, Gianluca, additional, İnanç, Murat, additional, Panopoulos, Stylianos, additional, Tandaipan, Jose‐Luis, additional, Chatelus, Emmanuel, additional, Rosato, Edoardo, additional, Kuwana, Masataka, additional, Yavuz, Sule, additional, Alegre‐Sancho, Juan J, additional, Smith, Vanessa, additional, Szűcs, Gabriella, additional, Henes, Joerg, additional, Rodríguez‐Pintó, Ignasi, additional, Atzeni, Fabiola, additional, Spierings, Julia, additional, Truchetet, Marie‐Elise, additional, Milchert, Marcin, additional, Brito de Araujo, Daniel, additional, Riemekasten, Gabriela, additional, Bernardino, Vera, additional, Martin, Thierry, additional, del Galdo, Francesco, additional, Vacca, Alessandra, additional, Mendoza, Fabian, additional, Midtvedt, Øyvind, additional, Murdaca, Giuseppe, additional, Santiago, Tânia, additional, Codullo, Veronica, additional, Cacciapaglia, Fabio, additional, Walker, Ulrich, additional, Brunborg, Cathrine, additional, Tirelli, Francesca, additional, Allanore, Yannick, additional, Furst, Daniel E., additional, Matucci, Marco, additional, Gabrielli, Armando, additional, Distler, Oliver, additional, and Hoffmann‐Vold, Anna‐Maria, additional
- Published
- 2023
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26. Chapter 42 - Infections and Systemic Sclerosis
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Balbir-Gurman, Alexandra and Braun-Moscovici, Yolanda
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- 2024
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27. An unexpected diagnosis of a 57-year-old women with migratory pulmonary infiltrates
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Mor, Elad, primary, Balbir-Gurman, Alexandra, additional, Guralnik, Ludmila, additional, Naroditski, Inna, additional, Zayoud, Morad, additional, and Dotan, Yaniv, additional
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- 2023
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28. Systemic sclerosis and primary biliary cholangitis: Longitudinal data to determine the outcomes
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Lepri, Gemma, primary, Airò, Paolo, additional, Distler, Oliver, additional, Andréasson, Kristofer, additional, Braun-Moscovici, Yolanda, additional, Hachulla, Eric, additional, Balbir-Gurman, Alexandra, additional, De Langhe, Ellen, additional, Rednic, Simona, additional, Ingegnoli, Francesca, additional, Rosato, Edoardo, additional, Groseanu, Laura, additional, Ionescu, Ruxandra, additional, Bellando-Randone, Silvia, additional, Garzanova, Liudmila, additional, Beretta, Lorenzo, additional, Bellocchi, Chiara, additional, Moiseev, Sergey, additional, Novikov, Pavel, additional, Szabo, Iulia, additional, Krasowska, Dorota, additional, Codullo, Veronica, additional, Walker, Ulrich A., additional, Manolaraki, Chrysoula, additional, Guiducci, Serena, additional, Truchetet, Marie-Elise, additional, Iannone, Florenzo, additional, Tofani, Lorenzo, additional, Bruni, Cosimo, additional, Smith, Vanessa, additional, Cuomo, Giovanna, additional, Krusche, Martin, additional, Matucci-Cerinic, Marco, additional, and Allanore, Yannick, additional
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- 2023
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29. An international SUrvey on non-iNvaSive tecHniques to assess the mIcrocirculation in patients with RayNaud’s phEnomenon (SUNSHINE survey)
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Ingegnoli, Francesca, Ughi, Nicola, Dinsdale, Graham, Orenti, Annalisa, Boracchi, Patrizia, Allanore, Yannick, Foeldvari, Ivan, Sulli, Alberto, Cutolo, Maurizio, Smith, Vanessa, Herrick, Ariane L., Hij, Adrian, Sulli, Alberto, Nitsche, Alejandro, Vacca, Alessandra, Balbir-Gurman, Alexandra, Abdessemed, Amina, Vargas, Angelica, Valenzuela, Antonia, Makol, Ashima, Baranauskaite, Asta, Derfalvi, Beata, Serrano Benavente, Belén, Sozeri, Betul, Bica, Blanca E., Stamenkovic, Bojana, Mihai, Carina, Chizzolini, Carlo, Abud Mendoza, Carlos, de la Puente, Carlos, von Muhlen, Carlos, Bertolazzi, Chiara, Pain, Clare, Ickinger, Claudia, Ancuta, Codrina, Sunderkotter, Cord, Kayser, Cristiane, De Araujo, Daniel B., Launay, David, Khanna, Dinesh, Krasowska, Dorota, Veale, Douglas, Kaliterna, Dušanka M., Rosato, Edoardo, de Langhe, Ellen, Hachulla, Eric, Naredo, Esperanza, Loyo, Esthela, Alvarez Hernández, Everardo, Sztajnbok, Flavio, Boin, Francesco, Longo, Francisco J., van den Hoogen, Frank, Hernandez Molina, Gabriela, Riemekasten, Gabriela, Szucs, Gabriella, Moroncini, Gianluca, Fragoso Loyo, Hilda, Dobrev, Hristo, Janta, Iustina, Cracowski, Jean-Luc, Pauling, John, Akikusa, Jonathan, Sotoca Fernàndez, Jorge, Khan Ajaz, Kariem, Solanki, Kamal, Wierzba, Karol, Romanowska Próchnicka, Katarzyna, Rouster Stevens, Kelly, Belloli, Laura, Lewandowski, Laura, Santos, Lelita, Saketkoo, Lesley A., Ananyeva, Lidia, Beretta, Lorenzo, Michalska Jakubus, Małgorzata, Audisio, Marcelo J., Milchert, Marcin, Molina, Maria J., Moraes, Fontes Maria F., Terreri, Maria T., Puszczewicz, Mariusz, Barešić, Marko, Hufnagel, Markus, Mamani, Marta N., Gutierrez, Marwin, Curran, Megan, Hughes, Michael, Becker, Mike, Inanç, Murat, Petraitis, Mykolas, Juan Carlos, Nieto-Gonzàlez, Fathi, Nihal, Aktay Ayaz, Nuray, Distler, Oliver, Sander, Oliver, Ömer, Pamuk N., García dela Peña Lefebvre, Paloma, Caramaschi, Paola, Hasler, Paul, Ostojic, Predrag, Bečvář, Radim, Rodríguez, Reyna S. Tatiana, Lima, Rodrigo, Hesselstrand, Roger, Cimaz, Rolando, Irace, Rosaria, Petty, Ross, de Angelis, Rossella, Dobrota, Rucsandra, Payne-Poff, Sarah, Kubo, Satoshi, Guiducci, Serena, Popa, Serghei, Lambova, Sevdalina, Stebbings, Simon, Rednic, Simona, Yavuz, Sule, Benseler, Susa, Shevtsova, Tatzana, Daikeler, Thomas, Schmeiser, Tim, Frech, Tracy, Minier, Tünde, Müller Ladner, Ulf, Walker, Ulrich, Riccieri, Valeria, Vilela, Verônica, Hermann, Walter, Braun-Moscovici, Yolanda, Uziel, Yosef, Thierry, Zenone, and On behalf of the EULAR Study Group on Microcirculation in RheumaticDiseases
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- 2017
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30. A deep look into the storm: Israeli multi-center experience of coronavirus disease 2019 (COVID-19) in patients with autoimmune inflammatory rheumatic diseases before and after vaccinations
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Kharouf, Fadi, primary, Eviatar, Tali, additional, Braun, Maya, additional, Pokroy-Shapira, Elisheva, additional, Brodavka, Michal, additional, Zloof, Yair, additional, Agmon-Levin, Nancy, additional, Toledano, Kochava, additional, Oren, Shirly, additional, Lidar, Merav, additional, Zisman, Devy, additional, Tavor, Yonit, additional, Amit-Vazina, Mirit, additional, Sabbah, Firas, additional, Breuer, Gabriel S., additional, Dagan, Amir, additional, Beshara-Garzuzi, Rima, additional, Markovits, Doron, additional, Elias, Muna, additional, Feld, Joy, additional, Tayer-Shifman, Oshrat, additional, Gazitt, Tal, additional, Reitblatt, Tatiana, additional, Rubin, Limor, additional, Haddad, Amir, additional, Giryes, Sami, additional, Paran, Daphna, additional, Peleg, Hagit, additional, Molad, Yair, additional, Elkayam, Ori, additional, Mevorach, Dror, additional, Balbir-Gurman, Alexandra, additional, and Braun-Moscovici, Yolanda, additional
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- 2023
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31. Phenotype of limited cutaneous systemic sclerosis patients with positive anti-topoisomerase I antibodies: data from EUSTAR cohort
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Zanatta, Elisabetta, Huscher, Dörte, Ortolan, Augusta, Avouac, Jérôme, Airó, Paolo, Balbir-Gurman, Alexandra, Siegert, Elise, Cerinic, Marco Matucci, Cozzi, Franco, Riemekasten, Gabriela, Hoffmann-Vold, Anna-Maria, Distler, Oliver, Gabrielli, Armando, Heitmann, Stefan, Hunzelmann, Nicolas, Montecucco, Carlomaurizio, Morovic-Vergles, Jadranka, Ribi, Camillo, Doria, Andrea, Allanore, Yannick, EUSTAR collaborators, and University of Zurich
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10051 Rheumatology Clinic and Institute of Physical Medicine ,610 Medicine & health - Published
- 2022
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32. Stratification in systemic sclerosis according to autoantibody status versus skin involvement: a study of the prospective EUSTAR cohort
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Elhai, Muriel, Sritharan, Nanthara, Boubaya, Marouane, Balbir-Gurman, Alexandra, Siegert, Elise, Hachulla, Eric, de Vries-Bouwstra, Jeska, Riemekasten, Gabriela, Distler, Jörg H W, Rosato, Edoardo, Del Galdo, Francesco, Mendoza, Fabian A, Furst, Daniel E, de la Puente, Carlos, Hoffmann-Vold, Anna-Maria, Gabrielli, Armando, Distler, Oliver, Bloch-Queyrat, Coralie, Allanore, Yannick, Matucci Cerinic, Marco, Walker, Ulrich, Iannone, Florenzo, Jordan, Suzana, Becvar, Radim, Kowal Bielecka, Otylia, Cutolo, Maurizio, Cuomo, Giovanna, Kedor, Claudia, Rednic, Simona, Avouac, Jérome, et al, University of Zurich, and Allanore, Yannick
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2403 Immunology ,Rheumatology ,2745 Rheumatology ,Immunology ,10051 Rheumatology Clinic and Institute of Physical Medicine ,2723 Immunology and Allergy ,Immunology and Allergy ,610 Medicine & health - Published
- 2022
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33. Stratification in systemic sclerosis according to autoantibody status versus skin involvement: a study of the prospective EUSTAR cohort
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Elhai, Muriel, primary, Sritharan, Nanthara, additional, Boubaya, Marouane, additional, Balbir-Gurman, Alexandra, additional, Siegert, Elise, additional, Hachulla, Eric, additional, de Vries-Bouwstra, Jeska, additional, Riemekasten, Gabriela, additional, Distler, Jörg H W, additional, Rosato, Edoardo, additional, Del Galdo, Francesco, additional, Mendoza, Fabian A, additional, Furst, Daniel E, additional, de la Puente, Carlos, additional, Hoffmann-Vold, Anna-Maria, additional, Gabrielli, Armando, additional, Distler, Oliver, additional, Bloch-Queyrat, Coralie, additional, Allanore, Yannick, additional, Matucci Cerinic, Marco, additional, Walker, Ulrich, additional, Iannone, Florenzo, additional, Jordan, Suzana, additional, Becvar, Radim, additional, Kowal Bielecka, Otylia, additional, Cutolo, Maurizio, additional, Cuomo, Giovanna, additional, Kedor, Claudia, additional, Rednic, Simona, additional, Avouac, Jérome, additional, Vlachoyiannopoulos, P., additional, Montecucco, C., additional, Stork, Jiri, additional, Inanc, Murat, additional, Carreira, Patricia E., additional, Novak, Srdan, additional, Czirják, László, additional, Iudici, Michele, additional, Kucharz, Eugene J., additional, Zanatta, Elisabetta, additional, Perdan-Pirkmajer, Katja, additional, Coleiro, Bernard, additional, Moroncini, Gianluca, additional, Farge Bancel, Dominique, additional, Airò, Paolo, additional, Hesselstrand, Roger, additional, Radic, Mislav, additional, Braun-Moscovici, Yolanda, additional, Lo Monaco, Andrea, additional, Hunzelmann, Nicolas, additional, Pellerito, Raffaele, additional, Giollo, Alessandro, additional, Morovic-Vergles, Jadranka, additional, Denton, Christopher, additional, Vonk, Madelon, additional, Damjanov, Nemanja, additional, Henes, Jörg, additional, Ortiz Santamaria, Vera, additional, Heitmann, Stefan, additional, Krasowska, Dorota, additional, Hasler, Paul, additional, Kohm, Michaela, additional, Foeldvari, Ivan, additional, Bajocchi, Gianluigi, additional, Salvador, Maria João, additional, Stamenkovic, Bojana, additional, Selmi, Carlo Francesco, additional, Tikly, Mohammed, additional, Ananieva, Lidia P., additional, Herrick, Ariane, additional, Müller-Ladner, Ulf, additional, De Palma, Raffaele, additional, Engelhart, Merete, additional, Szücs, Gabriela, additional, Sobrino Grande, Cristina, additional, Midtvedt, Øyvind, additional, Launay, David, additional, Riccieri, Valeria, additional, Ionescu, Ruxandra Maria, additional, Sha, Ami, additional, Gheorghiu, Ana Maria, additional, Sunderkötter, Cord, additional, Ingegnoli, Francesca, additional, Mouthon, Luc, additional, Smith, Vanessa, additional, Cantatore, Francesco Paolo, additional, Ullman, Susanne, additional, Alberto von Mühlen, Carlos, additional, Pozzi, Maria Rosa, additional, Eyerich, Kilian, additional, Wiland, Piotr, additional, Vanthuyne, Marie, additional, Alegre-Sancho, Juan Jose, additional, Herrmann, Kristine, additional, De Langhe, Ellen, additional, Anic, Branimir, additional, Üprus, Maria, additional, Yavuz, Sule, additional, Granel, Brigitte, additional, de Souza Müller, Carolina, additional, Busquets, Joanna, additional, Agachi, Svetlana, additional, Stebbings, Simon, additional, Mathieu, D'Alessandro, additional, Sampaio-Barros, Percival D., additional, Stamp, Lisa, additional, Solanki, Kamal, additional, Veale, Douglas, additional, Loyo, Esthela, additional, Li, Mengtao, additional, Abdel Atty Mohamed, Walid Ahmed, additional, Gigante, Antonietta, additional, Oksel, Fahrettin, additional, Tanaseanu, Cristina-Mihaela, additional, Foti, Rosario, additional, Ancuta, Codrina, additional, Maurer, Britta, additional, van Laar, Jacob, additional, Kayser, Cristiane, additional, Fathi, Nihal, additional, García de la Peña Lefebvre, Paloma, additional, Sibilia, Jean, additional, Litinsky, Ira, additional, Abignano, Giuseppina, additional, Seskute, Goda, additional, Saketkoo, Lesley Ann, additional, Kerzberg, Eduardo, additional, Bianchi, Washington, additional, Castellví, Ivan, additional, Limonta, Massimiliano, additional, Rimar, Doron, additional, Couto, Maura, additional, Spertini, François, additional, Marcoccia, Antonella, additional, Kahl, Sarah, additional, Hsu, Ivien M., additional, Martin, Thierry, additional, Moiseev, Sergey, additional, Chung, Lorinda S., additional, Schmeiser, Tim, additional, Majewski, Dominik, additional, Zdrojewski, Zbigniew, additional, Martínez-Barrio, Julia, additional, Bernardino, Vera, additional, Sommerlatte, Sabine, additional, Levy, Yair, additional, Rezus, Elena, additional, Nuri Pamuk, Omer, additional, Sarzi Puttini, Piercarlo, additional, Poormoghim, Hadi, additional, Kötter, Ina, additional, Gaches, Francis, additional, Belloli, Laura, additional, Sfikakis, Petros, additional, Markus, Juliana, additional, Feldman, Gary R, additional, Ramazan, Ana-Maria, additional, Scherer, H.U., additional, Truchetet, Marie-Elise, additional, Lescoat, Alain, additional, Dagna, Lorenzo, additional, van Laar, J.M., additional, Rudnicka, Lidia, additional, Oliveira, Susana, additional, Atzeni, Fabiola, additional, Kuwana, Masataka, additional, Mekinian, Arsene, additional, Martin, Mickaël, additional, and Tanaka, Yoshiya, additional
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- 2022
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34. Clinical characteristics of juvenile onset systemic sclerosis patients from the juvenile scleroderma inception cohort compared to adult age juvenile-onset patients from EUSTAR. Are these differences suggesting risk for mortality?
- Author
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Foeldvari, Ivan, Klotsche, Jens, Carreira, Patricia E., Kasapcopur, Ozgur, Adrovic, Amra, Torok, Kathryn, Airò, Paolo, Iannone, Florenzo, Allanore, Yannick, Balbir-Gurman, Alexandra, Schmeiser, Tim, Sztajnbok, Flavio, Terreri, Maria Teresa, Stanevicha, Valda, Anton, Jordi, Feldman, Brian, Khubchandani, Raju, Alexeeva, Ekaterina, Johnson, Sindhu, Katsicas, Maria, Sawhney, Sujata, Smith, Vanessa, Appenzeller, Simone, Avcin, Tadey, Campochiaro, Corrado, De Vries-Bouwstra, Jeska, Kostik, Mikhail, Lehman, Thomas, Marrani, Edoardo, Schonenberg, Dieneke, Sifuentes-Giraldo, W.-Alberto, Vasquez-Canizares, Natalia, Janarthanan, Mahesh, Malcova, Hana, Moll, Monika, Nemcova, Dana, Patwardhan, Anjali, Santos, Maria Jose, Seskute, Goda, Truchetet, Marie-Elise, Veale, Douglas, Hoffmann-Vold, Anna-Maria, Gabrielli, Armando, and Distler, Oliver
- Subjects
Medicine and health - Abstract
Introduction: Juvenile systemic sclerosis (jSSc) is an orphan autoimmune disease with a prevalence of 3 in 1,000,000 children. Information on long-term development of organ involvement and clinical characteristics of jSSc patients in adulthood are lacking. It was believed that patients in adult cohorts [for full text, please go to the a.m. URL]
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- 2022
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35. Mapping and predicting mortality from systemic sclerosis
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Elhai, Muriel, Meune, Christophe, Boubaya, Marouane, Avouac, Jérôme, Hachulla, Eric, Balbir-Gurman, Alexandra, Riemekasten, Gabriela, Airò, Paolo, Joven, Beatriz, Vettori, Serena, Cozzi, Franco, Ullman, Susanne, Czirják, László, Tikly, Mohammed, Müller-Ladner, Ulf, Caramaschi, Paola, Distler, Oliver, Iannone, Florenzo, Ananieva, Lidia P, Hesselstrand, Roger, Becvar, Radim, Gabrielli, Armando, Damjanov, Nemanja, Salvador, Maria J, Riccieri, Valeria, Mihai, Carina, Szücs, Gabriella, Walker, Ulrich A, Hunzelmann, Nicolas, Martinovic, Duska, Smith, Vanessa, Müller, Carolina de Souza, Montecucco, Carlo Maurizio, Opris, Daniela, Ingegnoli, Francesca, Vlachoyiannopoulos, Panayiotis G, Stamenkovic, Bojana, Rosato, Edoardo, Heitmann, Stefan, Distler, Jörg H W, Zenone, Thierry, Seidel, Matthias, Vacca, Alessandra, Langhe, Ellen De, Novak, Srdan, Cutolo, Maurizio, Mouthon, Luc, Henes, Jörg, Chizzolini, Carlo, Mühlen, Carlos Alberto von, Solanki, Kamal, Rednic, Simona, Stamp, Lisa, Anic, Branimir, Santamaria, Vera Ortiz, Santis, Maria De, Yavuz, Sule, Sifuentes-Giraldo, Walter Alberto, Chatelus, Emmanuel, Stork, Jiri, Laar, Jacob van, Loyo, Esthela, García de la Peña Lefebvre, Paloma, Eyerich, Kilian, Cosentino, Vanesa, Alegre-Sancho, Juan Jose, Kowal-Bielecka, Otylia, Rey, Grégoire, Matucci-Cerinic, Marco, and Allanore, Yannick
- Published
- 2017
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36. Severe hyperferritinemia—a clue for severe hepatitis in a patient with adult-onset Still’s disease
- Author
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Bishara, Rema, Braun-Moscovici, Yolanda, Dagan, Amir, Toledano, Kohava, Saadi, Tarek, Sabo, Edmond, and Balbir-Gurman, Alexandra
- Published
- 2016
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37. Ultrasound assessment of enthesis thickening in psoriatic arthritis patients treated with adalimumab compared to methotrexate
- Author
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Litinsky, Irena, Balbir-Gurman, Alexandra, Wollman, Jonathan, Arad, Uri, Paran, Daphna, Caspi, Dan, and Elkayam, Ori
- Published
- 2016
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38. The Role of CCL24 in Systemic Sclerosis.
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Levy, Hilit, Gluschnaider, Udi, and Balbir-Gurman, Alexandra
- Subjects
SYSTEMIC scleroderma ,PULMONARY fibrosis ,FIBROSIS ,CLINICAL trials ,EPITHELIAL cells ,PNEUMONIA - Abstract
Systemic sclerosis (SSc) is a chronic immune-mediated disease characterized by microangiopathy, immune dysregulation, and progressive fibrosis of the skin and internal organs. Though not fully understood, the pathogenesis of SSc is dominated by microvascular injury, endothelial dysregulation, and immune response that are thought to be associated with fibroblast activation and related fibrogenesis. Among the main clinical subsets, diffuse SSc (dSSc) is a progressive form with rapid and disseminated skin thickening accompanied by internal organ fibrosis and dysfunction. Despite recent advances and multiple randomized clinical trials in early dSSc patients, an effective disease-modifying treatment for progressive skin fibrosis is still missing, and there is a crucial need to identify new targets for therapeutic intervention. Eotaxin-2 (CCL24) is a chemokine secreted by immune cells and epithelial cells, which promotes trafficking of immune cells and activation of pro-fibrotic cells through CCR3 receptor binding. Higher levels of CCL24 and CCR3 were found in the skin and sera of patients with SSc compared with healthy controls; elevated levels of CCL24 and CCR3 were associated with fibrosis and predictive of greater lung function deterioration. Growing evidence supports the potency of a CCL24-blocking antibody as an anti-inflammatory and anti-fibrotic modulating agent in multiple preclinical models that involve liver, skin, and lung inflammation and fibrosis. This review highlights the role of CCL24 in orchestrating immune, vascular, and fibrotic pathways, and the potential of CCL24 inhibition as a novel treatment for SSc. [ABSTRACT FROM AUTHOR]
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- 2023
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39. Scleroderma – New aspects in pathogenesis and treatment
- Author
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Balbir-Gurman, Alexandra and Braun-Moscovici, Yolanda
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- 2012
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40. Environmental and societal factors associated with COVID-19-related death in people with rheumatic disease: an observational study
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Izadi, Zara, primary, Gianfrancesco, Milena A, additional, Schmajuk, Gabriela, additional, Jacobsohn, Lindsay, additional, Katz, Patricia, additional, Rush, Stephanie, additional, Ja, Clairissa, additional, Taylor, Tiffany, additional, Shidara, Kie, additional, Danila, Maria I, additional, Wysham, Katherine D, additional, Strangfeld, Anja, additional, Mateus, Elsa F, additional, Hyrich, Kimme L, additional, Gossec, Laure, additional, Carmona, Loreto, additional, Lawson-Tovey, Saskia, additional, Kearsley-Fleet, Lianne, additional, Schaefer, Martin, additional, Al-Emadi, Samar, additional, Sparks, Jeffrey A, additional, Hsu, Tiffany Y-T, additional, Patel, Naomi J, additional, Wise, Leanna, additional, Gilbert, Emily, additional, Duarte-García, Alí, additional, Valenzuela-Almada, Maria O, additional, Ugarte-Gil, Manuel F, additional, Ljung, Lotta, additional, Scirè, Carlo A, additional, Carrara, Greta, additional, Hachulla, Eric, additional, Richez, Christophe, additional, Cacoub, Patrice, additional, Thomas, Thierry, additional, Santos, Maria J, additional, Bernardes, Miguel, additional, Hasseli, Rebecca, additional, Regierer, Anne, additional, Schulze-Koops, Hendrik, additional, Müller-Ladner, Ulf, additional, Pons-Estel, Guillermo, additional, Tanten, Romina, additional, Nieto, Romina E, additional, Pisoni, Cecilia N, additional, Tissera, Yohana S, additional, Xavier, Ricardo, additional, Lopes Marques, Claudia D, additional, Pileggi, Gecilmara C S, additional, Robinson, Philip C, additional, Machado, Pedro M, additional, Sirotich, Emily, additional, Liew, Jean W, additional, Hausmann, Jonathan S, additional, Sufka, Paul, additional, Grainger, Rebecca, additional, Bhana, Suleman, additional, Gore-Massy, Monique, additional, Wallace, Zachary S, additional, Yazdany, Jinoos, additional, Dahou, Brahim, additional, Gómez, Gimena, additional, Roberts, Karen, additional, Baez, Roberto M, additional, Castro Coello, Vanessa V, additional, Haye Salinas, María J, additional, Maldonado, Federico N, additional, Reyes, Alvaro A, additional, Alle, Gelsomina, additional, Maldonado Ficco, Hernán, additional, Nieto, Romina, additional, Gobbi, Carla, additional, Tissera, Yohana, additional, Pisoni, Cecilia, additional, Paula, Alba, additional, Albiero, Juan A, additional, Schmid, Maria M, additional, Cosatti, Micaela, additional, Gamba, Maria J, additional, Leandro, Carlevaris, additional, Cusa, María A, additional, German, Noelia, additional, Bellomio, Veronica, additional, Takashima, Lorena, additional, Pera, Mariana, additional, Cogo, Karina, additional, Gálvez Elkin, Maria S, additional, Medina, María A, additional, Savio, Veronica, additional, Rojas Tessel, Romina, additional, Alamino, Rodolfo P, additional, Werner, Marina L, additional, Ornella, Sofía, additional, Casalla, Luciana, additional, de la Vega, Maria, additional, Severina, María, additional, García, Mercedes, additional, Gonzalez Lucero, Luciana, additional, Romeo, Cecilia, additional, Moyano, Sebastián, additional, Barbich, Tatiana, additional, Bertoli, Ana, additional, Baños, Andrea, additional, Petruzzelli, Sandra, additional, Matellan, Carla, additional, Conti, Silvana, additional, Lazaro, Maria A, additional, Rodriguez Gil, Gustavo F, additional, Risueño, Fabian, additional, Quaglia, Maria I, additional, Scafati, Julia, additional, Cuchiaro, Natalia L, additional, Rebak, Jonathan E, additional, Pineda, Susana I, additional, Calvo, María E, additional, Picco, Eugenia, additional, Yanzi, Josefina G, additional, Maid, Pablo, additional, Guaglianone, Debora, additional, Morbiducci, Julieta S, additional, Porta, Sabrina, additional, Herscovich, Natalia, additional, Velasco Zamora, José L, additional, Kisluk, Boris, additional, Castaños Menescardi, Maria S, additional, Gallo, Rosana, additional, Martire, María V, additional, Maldini, Carla, additional, Goizueta, Cecilia, additional, de la Vega Fernandez, Sabrina S, additional, Aeschlimann, Carolina, additional, Subils, Gisela, additional, Rath, Eva, additional, Piette, Yves, additional, Devinck, Mieke, additional, Maeyaert, Bea, additional, Machado Ribeiro, Francinne, additional, Euzebio Ribeiro, Sandra L, additional, Pinheiro, Marcelo, additional, Ibáñez, Sebastián, additional, Chassin Trubert, Anne-Marie, additional, Dong, Lingli, additional, Cajas, Lui, additional, Barešić, Marko, additional, Anić, Branimir, additional, Ćulo, Melanie-Ivana, additional, Pavelić, Tea A, additional, Stranski, Kristina K, additional, Karanovic, Boris, additional, Vencovsky, Jiri, additional, Píchová, Marta, additional, Filkova, Maria, additional, Hamoud, Hesham, additional, Vassilopoulos, Dimitrios, additional, Guzman Melgar, Gabriela M, additional, So, Ho, additional, Király, Márta, additional, Vojdanian, Mahdi, additional, Balbir Gurman, Alexandra, additional, Abutiban, Fatemah, additional, Zepa, Julija, additional, Bulina, Inita, additional, Bukauskiene, Loreta, additional, Zazueta Montiel, Beatriz E, additional, Castillo Ortiz, Angel A, additional, Zamora Tehozol, Erick, additional, Vega Morales, David, additional, Cervántes Rosete, Diana, additional, Martín Nares, Eduardo, additional, Rodriguez Reyna, Tatiana S, additional, Rull Gabayet, Marina, additional, Alpízar Rodríguez, Deshiré, additional, Irazoque, Fedra, additional, Jimenez, Xochitl, additional, Geurts van Bon, Lenny, additional, Zijlstra, Theo, additional, Hoekstra, Monique, additional, Al Adhoubi, Nasra, additional, Salim, Babur, additional, Giraldo, Enrique, additional, Salinas, Ariel, additional, Ugarte Gil, Manuel, additional, Nowakowski, Jarosław, additional, Conway, Richard, additional, Flood, Rachael, additional, McCarthy, Geraldine, additional, Felea, Ioana, additional, Filipescu, Ileana, additional, Rednic, Simona, additional, Groseanu, Laura, additional, Tamas, Maria M, additional, Mlynarikova, Vanda, additional, Skamlova, Martina, additional, Zlnay, Martin, additional, Mičeková, Dagmar, additional, Capova, Lubica, additional, Macejova, Zelmira, additional, Šteňová, Emőke, additional, Raffayova, Helena, additional, Belakova, Gabriela, additional, Strakova, Eva, additional, Senčarová, Marieta, additional, Žlnayová, Soňa, additional, Sabová, Anna, additional, Spisakova, Daniela, additional, Oetterová, Mária, additional, Lukacova, Olga, additional, Bakosova, Martina, additional, Hocevar, Alojzija, additional, de la Torre Rubio, Natalia, additional, Alegre Sancho, Juan J, additional, Corteguera Coro, Montserrat, additional, Cobeta Garcia, Juan C, additional, Torres Martin, Maria C, additional, Campos, Jose, additional, Gomez Puerta, Jose A, additional, Yardimci, Gozd K, additional, Akar, Servet, additional, Icacan, Ozan C, additional, ÇELİK, Selda, additional, Vasylets, Viktoriia, additional, Yeoh, Su-Ann, additional, Vandevelde, Claire, additional, Dunt, Sasha, additional, Leeder, Jane, additional, Macphie, Elizabeth, additional, Salerno, Rosaria, additional, Graver, Christine, additional, Williams, Katie, additional, O'Reilly, Sheila, additional, Devine, Kirsty, additional, Tyler, Jennifer, additional, Warner, Elizabeth, additional, Pilcher, James, additional, Patel, Samir, additional, Nikiphorou, Elena, additional, Chadwick, Laura, additional, Jones, Caroline M, additional, Harrison, Beverley, additional, Thornton, Lucy, additional, O'Kane, Diana, additional, Fusi, Lucia, additional, Low, Audrey, additional, Horton, Sarah, additional, Jatwani, Shraddha, additional, Baig, Sara, additional, Bajwa, Hammad, additional, Berglund, Vernon, additional, Dahle, Angela, additional, Dorman, Walter, additional, Hargrove, Jody, additional, Hilton, Maren, additional, Lebedoff, Nicholas, additional, Leonard, Susan, additional, Morgan, Jennifer, additional, Pfeifer, Emily, additional, Skemp, Archibald, additional, Wilson, Jeffrey, additional, Wolff, Anne, additional, Cepeda, Eduardo, additional, Todd, Derrick, additional, Hare, Denise, additional, Calabrese, Cassandra, additional, Adams, Christopher, additional, Khosroshahi, Arezou, additional, Kilian, Adam, additional, White, Douglas, additional, Winter, Melanie, additional, Fields, Theodore, additional, Siegel, Caroline, additional, Daver, Nicole, additional, Harvey, Melissa, additional, Kramer, Neil, additional, Lamore, Concetta, additional, Hogarty, Suneya, additional, Yeter, Karen, additional, Siddique, Faizah, additional, Ban, Byung, additional, Tanner, Tamar, additional, Ruderman, Eric, additional, Davis, William, additional, Quinet, Robert, additional, Scopelitis, Evangeline, additional, Toribio, Karen, additional, Webb Detiege, Tameka, additional, Zakem, Jerald, additional, Abbass, Khurram, additional, Kepecs, Gilbert, additional, Miranda, Lilliam, additional, Guma, Michael, additional, Haikal, Ammar, additional, Mody, Sushama, additional, Mueller, Daric, additional, Jayatilleke, Arundathi, additional, Zell, JoAnn, additional, Bays, Alison, additional, Dao, Kathryn, additional, Ezzati, Fatemeh, additional, Parks, Deborah, additional, Karp, David, additional, and Quiceno, Guillermo, additional
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- 2022
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41. Prediction of improvement in skin fibrosis in diffuse cutaneous systemic sclerosis: a EUSTAR analysis
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Dobrota, Rucsandra, Maurer, Britta, Graf, Nicole, Jordan, Suzana, Mihai, Carina, Kowal-Bielecka, Otylia, Allanore, Yannick, Distler, Oliver, Cerinic, Marco Matucci, Guiducci, Serena, Walker, Ulrich, Lapadula, Giovanni, Iannone, Florenzo, Becvar, Radim, Sierakowsky, Stanislaw, Cutolo, Maurizio, Sulli, Alberto, Valentini, Gabriele, Cuomo, Giovanna, Vettori, Serena, Riemekasten, Gabriela, Siegert, Elise, Rednic, Simona, Nicoara, Ileana, Kahan, André, Vlachoyiannopoulos, P., Montecucco, C., Caporali, Roberto, Carreira, Patricia E., Novak, Srdan, Czirják, László, Varju, Cecilia, Chizzolini, Carlo, Kucharz, Eugene J., Kotulska, Anna, Kopec-Medrek, Magdalena, Widuchowska, Malgorzata, Cozzi, Franco, Rozman, Blaz, Mallia, Carmel, Coleiro, Bernard, Gabrielli, Armando, Farge, Dominique, Wu, Chen, Marjanovic, Zora, Faivre, Helene, Hij, Darin, Dhamadi, Roza, Airò, Paolo, Hesselstrand, Roger, Wollheim, Frank, Wuttge, Dirk M, Andréasson, Kristofer, Martinovic, Duska, Balbir-Gurman, Alexandra, Braun-Moscovici, Yolanda, Trotta, F., Lo Monaco, Andrea, Hunzelmann, Nicolas, Pellerito, Raffaele, Mauriziano, Ospedale, Bambara, Lisa Maria, Caramaschi, Paola, Black, Carol, Denton, Christopher, Damjanov, Nemanja, Henes, Jörg, Ortiz Santamaria, Vera, Heitmann, Stefan, Krasowska, Dorota, Seidel, Matthias, Burkhardt, Harald, Himsel, Andrea, Salvador, Maria J., Silva, José Antonio Pereira Da, Stamenkovic, Bojana, Stankovic, Aleksandra, Banja, Niska, Tikly, Mohammed, Ananieva, Lidia P., Denisov, Lev N., Müller-Ladner, Ulf, Frerix, Marc, Tarner, Ingo, Scorza, Raffaella, Clinica, U.O. Immunologia, Engelhart, Merete, Strauss, Gitte, Nielsen, Henrik, Damgaard, Kirsten, Mendoza, Antonio Zea, de la Puente, Carlos, Giraldo, Walter A. Sifuentes, Midtvedt, Øyvind, Reiseter, Silje, Hachulla, Eric, Launay, David, Valesini, Guido, Riccieri, Valeria, Ionescu, Ruxandra Maria, Opris, Daniela, Groseanu, Laura, Cornateanu, Roxana Sfrent, Ionitescu, Razvan, Gherghe, Ana Maria, Soare, Alina, Gorga, Marilena, Bojinca, Mihai, Schett, Georg, Distler, Jörg HW, Beyer, Christian, Meroni, Pierluigi, Ingegnoli, Francesca, Mouthon, Luc, De Keyser, Filip, Smith, Vanessa, Cantatore, Francesco P., Corrado, Ada, Pozzi, Maria R., Eyerich, Kilian, Hein, Rüdiger, Knott, Elisabeth, Wiland, Piotr, Szmyrka-Kaczmarek, Magdalena, Sokolik, Renata, Morgiel, Ewa, Madej, Marta, Krummel-Lorenz, Brigitte, Aringer, Martin, Günther, Claudia, Westhovens, Rene, de Langhe, Ellen, Lenaerts, Jan, Anic, Branimir, Baresic, Marko, Mayer, Miroslav, Radominski, Sebastião C., de Souza Müller, Carolina, Azevedo, Valderílio F., Agachi, Svetlana, Groppa, Liliana, Chiaburu, Lealea, Russu, Eugen, Popa, Sergei, Zenone, Thierry, Highton, John, Stamp, Lisa, Chapman, Peter, O’Donnell, John, Solanki, Kamal, Veale, Douglas, OʼRourke, Marie, Loyo, Esthela, Li, Mengtao, Rosato, Edoardo, Amoroso, Antonio, Tanaseanu, Cristina-Mihaela, Popescu, Monica, Dumitrascu, Alina, Tiglea, Isabela, Foti, Rosario, Chirieac, Rodica, Ancuta, Codrina, Villiger, Peter, Adler, Sabine, Sibilia, Jean, Chatelus, Emmanuel, Gottenberg, Jacques Eric, Chifflot, Hélène, Litinsky, Ira, Venalis, Algirdas, Butrimiene, Irena, Venalis, Paulius, Rugiene, Rita, Karpec, Diana, Saketkoo, Lesley Ann, Lasky, Joseph A., Kerzberg, Eduardo, Montoya, Fabiana, Cosentino, Vanesa, Limonta, Massimiliano, Brucato, Antonio Luca, Lupi, Elide, Spertini, François, Ribi, Camillo, Buss, Guillaume, Pasquali, Jean Louis, Martin, Thierry, and Gorse, Audrey
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- 2016
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42. Digital pitting scars are associated with a severe disease course and death in systemic sclerosis: a study from the EUSTAR cohort
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Hughes, Michael, Heal, Calvin, Henes, Joerg, Balbir-Gurman, Alexandra, Distler, Jorg H. W., Airo, Paolo, Mueller-Ladner, Ulf, Hunzelmann, Nicolas, Kerzberg, Eduardo, Rudnicka, Lidia, Truchetet, Marie-Elise, Stebbings, Simon, Tanaka, Yoshiya, Hoffman-Vold, Anna Maria, Gabrielli, Armando, Distler, Oliver, Matucci-Cerinic, Marco, Hughes, Michael, Heal, Calvin, Henes, Joerg, Balbir-Gurman, Alexandra, Distler, Jorg H. W., Airo, Paolo, Mueller-Ladner, Ulf, Hunzelmann, Nicolas, Kerzberg, Eduardo, Rudnicka, Lidia, Truchetet, Marie-Elise, Stebbings, Simon, Tanaka, Yoshiya, Hoffman-Vold, Anna Maria, Gabrielli, Armando, Distler, Oliver, and Matucci-Cerinic, Marco
- Abstract
Objective Digital pitting scars (DPS) are frequent, but little studied in SSc to date. Methods An analysis of SSc patients enrolled in the EUSTAR database. Primary objectives were to (i) examine DPS prevalence; (ii) examine whether DPS are associated with digital ulcers (DUs) and active digital ischaemia (DUs or gangrene); and (iii) describe other associations with DPS including internal organ complications. Secondary objectives were whether DPS are associated with (i) functional impairment; (ii) structural microvascular disease; and (iii) mortality. Descriptive statistics and parametric/non-parametric tests were used. Binary logistic regression was used to examine the association between DPS and DUs, active digital ischaemia and mortality. Results A total of 9671 patients were included with reported DPS at any time point (n = 4924) or 'never' DPS (n = 4747). The majority (86.9%) were female and mean age was 55.7 years. DPS were associated with longer disease and Raynaud's duration (both P <= 0.001). DPS were associated with interstitial lung disease, pulmonary hypertension, conduction blocks, telangiectases, calcinosis (all P <= 0.001) and joint synovitis (P = 0.021). Patients were more likely to have more severe capillaroscopic abnormality and greater hand functional impairment. Multivariable logistic regression analyses showed that DPS were associated (odds ratio) with DUs: 22.03 (19.51-24.87), active digital ischaemia: 6.30 (5.34-7.42) and death: 1.86 (1.48-2.36). Conclusion DPS are associated with a severe disease course including death. The impact of DPS on hand function and ischaemia is significant. The presence of DPS should alert the clinician to a poor prognosis and need to optimize the therapeutic strategy.
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- 2022
43. Phenotype of limited cutaneous systemic sclerosis patients with positive anti-topoisomerase I antibodies: data from the EUSTAR cohort
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Zanatta, Elisabetta, Huscher, Doerte, Ortolan, Augusta, Avouac, Jerome, Airo, Paolo, Balbir-Gurman, Alexandra, Siegert, Elise, Cerinic, Marco Matucci, Cozzi, Franco, Riemekasten, Gabriela, Hoffmann-Vold, Anna-Maria, Distler, Oliver, Gabrielli, Armando, Heitmann, Stefan, Hunzelmann, Nicolas, Montecucco, Carlomaurizio, Morovic-Vergles, Jadranka, Ribi, Camillo, Doria, Andrea, Allanore, Yannick, Zanatta, Elisabetta, Huscher, Doerte, Ortolan, Augusta, Avouac, Jerome, Airo, Paolo, Balbir-Gurman, Alexandra, Siegert, Elise, Cerinic, Marco Matucci, Cozzi, Franco, Riemekasten, Gabriela, Hoffmann-Vold, Anna-Maria, Distler, Oliver, Gabrielli, Armando, Heitmann, Stefan, Hunzelmann, Nicolas, Montecucco, Carlomaurizio, Morovic-Vergles, Jadranka, Ribi, Camillo, Doria, Andrea, and Allanore, Yannick
- Abstract
Objectives To characterize patients with positive anti-topoisomerase I (ATA) in lcSSc. Methods SSc patients enrolled in the EUSTAR cohort with a disease duration of <= 3 years at database entry were considered. We assessed the risk of major organ involvement in the following groups: ATA-lcSSc vs ACA-lcSSc and vs ANA without specificity (ANA)-lcSSc, and ATA-lcSSc vs ATA-dcSSc. Cox regression models with time-dependent covariates were performed with the following outcomes: new-onset interstitial lung disease (ILD), ILD progression [forced vital capacity (FVC) decline >= 10% and >= 5% vs values at ILD diagnosis), primary myocardial involvement (PMI), pulmonary hypertension (PH), any organ involvement and all-cause mortality. Results We included 1252 patients [194 ATA-lcSSc (15.5%)], with 7.7 years (s.d. 3.5) of follow-up. ILD risk was higher in ATA-lcSSc vs ACA- and ANA-lcSSc and similar to ATA-dcSSc, although with less frequent restrictive lung disease. The risk of FVC decline >= 10% (35% of ATA-lcSSc) was lower in ATA-lcSSc than in ATA-dcSSc, whereas FVC decline >= 5% occurs similarly between ATA-lcSSc (58% of patients) and other SSc subsets, including ATA-dcSSc. The risk of PMI was similar in ATA-lcSSc and ANA-lcSSc but lower than in ACA-lcSSc; no difference in PH and mortality risk was observed among lcSSc subsets. The risk of any organ involvement, PMI and PH was lower and the mortality tended to be lower in ATA-lcSSc vs ATA-dcSSc. Conclusion ATA-lcSSc patients have a high risk of ILD, albeit with a lower risk of progression compared with ATA-dcSSc, supporting careful screening for ILD in this subgroup.
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- 2022
44. Digital pitting scars are associated with a severe disease course and death in systemic sclerosis: a study from the EUSTAR cohort (vol 61, pg 1141, 2022)
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Hughes, Michael, Heal, Calvin, Henes, Joerg, Balbir-Gurman, Alexandra, Distler, Jorg H. W., Airo, Paolo, Mueller-Ladner, Ulf, Hunzelmann, Nicolas, Kerzberg, Eduardo, Rudnicka, Lidia, Truchetet, Marie-Elise, Stebbings, Simon, Tanaka, Yoshiya, Hoffman-Vold, Anna Maria, Gabrielli, Armando, Distler, Oliver, Matucci-Cerinic, Marco, Hughes, Michael, Heal, Calvin, Henes, Joerg, Balbir-Gurman, Alexandra, Distler, Jorg H. W., Airo, Paolo, Mueller-Ladner, Ulf, Hunzelmann, Nicolas, Kerzberg, Eduardo, Rudnicka, Lidia, Truchetet, Marie-Elise, Stebbings, Simon, Tanaka, Yoshiya, Hoffman-Vold, Anna Maria, Gabrielli, Armando, Distler, Oliver, and Matucci-Cerinic, Marco
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- 2022
45. Representativeness of Systemic Sclerosis Patients in Interventional Randomized Trials: an analysis of the EUSTAR database
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Iudici, Michele, Jarlborg, Matthias, Lauper, Kim; https://orcid.org/0000-0002-4315-9009, Müller-Ladner, Ulf, Smith, Vanessa; https://orcid.org/0000-0001-6271-7945, Allanore, Yannick; https://orcid.org/0000-0002-6149-0002, Balbir-Gurman, Alexandra, Doria, Andrea, Airò, Paolo, Walker, Ulrich A; https://orcid.org/0000-0002-9183-550X, Riccieri, Valeria, Vonk, Madelon C; https://orcid.org/0000-0002-2266-9907, Gabrielli, Armando, Hoffmann-Vold, Anna-Maria; https://orcid.org/0000-0001-6467-7422, Szücs, Gabriella, Martin, Thierry, Distler, Oliver; https://orcid.org/0000-0002-0546-8310, Courvoisier, Delphine S, EUSTAR collaborators, Iudici, Michele, Jarlborg, Matthias, Lauper, Kim; https://orcid.org/0000-0002-4315-9009, Müller-Ladner, Ulf, Smith, Vanessa; https://orcid.org/0000-0001-6271-7945, Allanore, Yannick; https://orcid.org/0000-0002-6149-0002, Balbir-Gurman, Alexandra, Doria, Andrea, Airò, Paolo, Walker, Ulrich A; https://orcid.org/0000-0002-9183-550X, Riccieri, Valeria, Vonk, Madelon C; https://orcid.org/0000-0002-2266-9907, Gabrielli, Armando, Hoffmann-Vold, Anna-Maria; https://orcid.org/0000-0001-6467-7422, Szücs, Gabriella, Martin, Thierry, Distler, Oliver; https://orcid.org/0000-0002-0546-8310, Courvoisier, Delphine S, and EUSTAR collaborators
- Abstract
OBJECTIVE: To estimate the extent of and the reasons for ineligibility in randomized controlled trials (RCTs) of systemic sclerosis (SSc) patients included in the EUSTAR database, and to determine the association between patient's features and generalizability of study results. METHODS: We searched Clinicaltrials.gov for all records on interventional SSc-RCTs registered from January 2013 to January 2018. Two reviewers selected studies, and information on the main trial features were retrieved. Data from 8046 patients having a visit in the EUSTAR database since 2013 were used to check patient's eligibility. The proportion of potentially eligible patients per trial, and the risk factors for ineligibility were analyzed. Complete-, worst- and best-case analyses were performed. RESULTS: Of the 37 RCTs included, 43% were conducted in Europe, 35% were industry-funded, and 87% investigated pharmacological treatments. Ninety-one percent of 8046 patients included could have participated in at least one RCT. In complete-case analysis, the median [range] proportion of eligible patients having the main organ complication targeted by each study was 60% [10-100] in the overall sample of trials, ranging from 50% [32-79] for trials on skin fibrosis to 90% [34-77] for those targeting Raynaud's phenomenon. Among the criteria checked, treatment- and safety-related but not demographic were the main barriers to patient's recruitment. Older age, absence of Raynaud's phenomenon, and lower mRSS were independently associated with the failure to fulfill criteria for any of the included studies. CONCLUSIONS: Patient's representativeness in SSc-RCTs is highly variable and is driven more by treatment- and safety-related rather than demographic criteria.
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- 2022
46. Pulmonary Arteries Involvement in Takayasu's Arteritis: Two Cases and Literature Review
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Toledano, Kohava, Guralnik, Ludmila, Lorber, Avraham, Ofer, Amos, Yigla, Mordechai, Rozin, Alexander, Markovits, Doron, Braun-Moscovici, Yolanda, and Balbir-Gurman, Alexandra
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- 2011
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47. Gonadotropin Releasing Hormone Agonists May Minimize Cyclophosphamide Associated Gonadotoxicity in SLE and Autoimmune Diseases
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Blumenfeld, Zeev, Mischari, Or, Schultz, Naomi, Boulman, Nina, and Balbir-Gurman, Alexandra
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- 2011
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48. Anti-Neutrophil Antibody Associated Vasculitis in Systemic Sclerosis
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Arad, Uri, Balbir-Gurman, Alexandra, Doenyas-Barak, Keren, Amit-Vazina, Mirit, Caspi, Dan, and Elkayam, Ori
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- 2011
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49. Hypocomplementemia during tocilizumab treatment
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Bieber, Amir, primary, Markovits, Doron, additional, Toledano, Kohava, additional, Tavor, Yonit, additional, Mader, Reuven, additional, Balbir-Gurman, Alexandra, additional, and Braun-Moscovici, Yolanda, additional
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- 2022
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50. Predictors of Immunogenic Response to the BNT162b2 mRNA COVID-19 Vaccination in Patients with Autoimmune Inflammatory Rheumatic Diseases Treated with Rituximab
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Furer, Victoria, primary, Eviatar, Tali, additional, Zisman, Devy, additional, Peleg, Hagit, additional, Braun-Moscovici, Yolanda, additional, Balbir-Gurman, Alexandra, additional, Paran, Daphna, additional, Levartovsky, David, additional, Zisapel, Michael, additional, Elalouf, Ofir, additional, Kaufman, Ilana, additional, Broyde, Adi, additional, Polachek, Ari, additional, Feld, Joy, additional, Haddad, Amir, additional, Gazitt, Tal, additional, Elias, Muna, additional, Higazi, Nizar, additional, Kharouf, Fadi, additional, Pel, Sara, additional, Nevo, Sharon, additional, and Elkayam, Ori, additional
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- 2022
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