1. Identification and Optimization of RNA-Splicing Modulators as Huntingtin Protein-Lowering Agents for the Treatment of Huntington’s Disease
- Author
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Liu, Longbin, primary, Malagu, Karine, additional, Haughan, Alan F., additional, Khetarpal, Vinod, additional, Stott, Andrew J., additional, Esmieu, William, additional, Vater, Huw D., additional, Webster, Stephen J., additional, Van de Poël, Amanda J., additional, Clissold, Cole, additional, Cosgrove, Brett, additional, Sutton, Benjamin, additional, Spencer, Jonathan A., additional, Breccia, Perla, additional, Gancia, Emanuela, additional, Bonomo, Silvia, additional, Ladduwahetty, Tammy, additional, Lazari, Ovadia, additional, Patel, Hiral, additional, Atton, Helen C., additional, Clifton, Steve, additional, Mota, Daniel M., additional, Magnani, Dario, additional, O’Neill, Amy, additional, Stebbeds, Marta, additional, Macabuag, Natsuko, additional, Todd, Daniel, additional, Herva, Maria E., additional, Mitchell, Philip, additional, Visser, Mijke, additional, Compte Sancerni, Sara, additional, Grand Moursel, Laure, additional, da Silva, Marta, additional, Kritikou, Eva, additional, Heikkinen, Taneli T., additional, Bolkvadze, Tamuna, additional, Fodale, Valentina, additional, Spadafora, Debora, additional, Daldin, Manuel, additional, Bresciani, Alberto, additional, Mangette, John E., additional, Doherty, Elizabeth M., additional, Lee, Matthew R., additional, Herbst, Todd, additional, Monteagudo, Edith, additional, Macdonald, Douglas, additional, Plotnikov, Nikolay V., additional, Chambers, Mark, additional, McAllister, George, additional, Muňoz-Sanjuan, Ignacio, additional, and Dominguez, Celia, additional
- Published
- 2023
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