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Your search keyword '"FETAL hemoglobin"' showing total 11,950 results

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11,950 results on '"FETAL hemoglobin"'

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1. Development and IND-enabling studies of a novel Cas9 genome-edited autologous CD34+ cell therapy to induce fetal hemoglobin for sickle cell disease

6. Ex vivo culture resting time impacts transplantation outcomes of genome-edited human hematopoietic stem and progenitor cells in xenograft mouse models

7. Base editing of key residues in the BCL11A-XL-specific zinc finger domains derepresses fetal globin expression

14. Editing the core region in HPFH deletions alters fetal and adult globin expression for treatment of β-hemoglobinopathies

16. Forced enhancer-promoter rewiring to alter gene expression in animal models

18. New Treatments for Sickle Cell Disease.

19. Living with Sickle Cell Disease.

24. Zinc finger nuclease-mediated gene editing in hematopoietic stem cells results in reactivation of fetal hemoglobin in sickle cell disease.

30. Structural dynamics of the heme pocket and intersubunit coupling in the dimeric hemoglobin from Scapharca inaequivalvis.

31. Epigenetic inactivation of ERF reactivates γ-globin expression in β-thalassemia

39. Changing the Story.

43. Preclinical Evaluation of a Novel Lentiviral Vector Driving Lineage-Specific BCL11A Knockdown for Sickle Cell Gene Therapy

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