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3. A biallelic variant in COX18 cause isolated Complex IV deficiency associated with neonatal encephalo-cardio-myopathy and axonal sensory neuropathy

6. Respiratory function in a large cohort of treatment-naïve adult spinal muscular atrophy patients: a cross-sectional study

8. Multi-omics profiling of CSF from spinal muscular atrophy type 3 patients after nusinersen treatment: a 2-year follow-up multicenter retrospective study

10. Guanylate Kinase 1 Deficiency: A Novel and Potentially Treatable Mitochondrial DNA Depletion/Deletions Disease.

11. Six‐minute walk test as outcome measure of fatigability in adults with spinal muscular atrophy treated with nusinersen.

12. Safety and efficacy of once-daily risdiplam in type 2 and non-ambulant type 3 spinal muscular atrophy (SUNFISH part 2): a phase 3, double-blind, randomised, placebo-controlled trial

13. Unleashing the potential of mRNA therapeutics for inherited neurological diseases

14. Investigating the prevalence of MFN2 mutations in amyotrophic lateral sclerosis: insights from an Italian cohort.

15. Insights into the identification of a molecular signature for amyotrophic lateral sclerosis exploiting integrated microRNA profiling of iPSC-derived motor neurons and exosomes

17. Lafora Disease: A Case Report and Evolving Treatment Advancements

18. Unraveling the Neurological Complexity of Polyneuropathy, Organomegaly, Endocrinopathy, Monoclonal Protein, and Skin Changes Syndrome: A Report of a Challenging Case of a Young Woman and Cutting-Edge Advancements in the Field

19. The impact of upper motor neuron involvement on clinical features, disease progression and prognosis in amyotrophic lateral sclerosis

20. Primary mitochondrial myopathy: Clinical features and outcome measures in 118 cases from Italy

23. Clinical and molecular features of patients with amyotrophic lateral sclerosis and SOD1 mutations: a monocentric study

24. Identification of Novel Biomarkers of Spinal Muscular Atrophy and Therapeutic Response by Proteomic and Metabolomic Profiling of Human Biological Fluid Samples

25. Regional spreading pattern is associated with clinical phenotype in amyotrophic lateral sclerosis

27. Analysis of miRNA rare variants in amyotrophic lateral sclerosis and in silico prediction of their biological effects

29. Adults with spinal muscular atrophy: a large-scale natural history study shows gender effect on disease

30. Correlation between clinical phenotype and electromyographic parameters in amyotrophic lateral sclerosis

33. Case Report: Rare Homozygous RNASEH1 Mutations Associated With Adult-Onset Mitochondrial Encephalomyopathy and Multiple Mitochondrial DNA Deletions

37. Biallelic Variants in ENDOG Associated with Mitochondrial Myopathy and Multiple mtDNA Deletions

39. Safety and efficacy of once-daily risdiplam in type 2 and non-ambulant type 3 spinal muscular atrophy (SUNFISH part 2): a phase 3, double-blind, randomised, placebo-controlled trial

41. 6MWT as measure of motor function and endurance in SMA type 3 patients treated with nusinersen

44. Impact of COVID‐19 on the quality of life of patients with neuromuscular disorders in the L ombardy area, I taly

45. A biallelic variant in COX18cause isolated Complex IV deficiency associated with neonatal encephalo-cardio-myopathy and axonal sensory neuropathy

46. Charcot–Marie–Tooth disease type 2F associated with biallelic HSPB1 mutations

48. Primary mitochondrial myopathy

49. Nusinersen safety and effects on motor function in adult spinal muscular atrophy type 2 and 3

50. TYMP Variants Result in Late-Onset Mitochondrial Myopathy With Altered Muscle Mitochondrial DNA Homeostasis

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