641 results on '"Ohashi, Toya"'
Search Results
2. Usefulness of antibody-drug conjugate as preconditioning for hematopoietic stem cell-targeted gene therapy in wild-type and Fabry disease mouse models
3. A novel preclinical model of mucopolysaccharidosis type II for developing human hematopoietic stem cell gene therapy
4. Hematopoietic stem cell gene therapy ameliorates CNS involvement in murine model of GM1-gangliosidosis
5. The role of native T1 values on the evaluation of cardiac manifestation in Japanese Fabry disease patients
6. Oral pharmacological chaperone migalastat compared with enzyme replacement therapy in Fabry disease: 18-month results from the randomised phase III ATTRACT study
7. Cross‐sectional study to identify health literacy, health behavior, and quality of life in Chofu and Komae cities in Japan: Formative research in community‐based nursing practice.
8. Ex Vivo Gene Therapy Treats Bone Complications of Mucopolysaccharidosis Type II Mouse Models through Bone Remodeling Reactivation
9. Long-term efficacy and safety of migalastat treatment in Fabry disease: 30-month results from the open-label extension of the randomized, phase 3 ATTRACT study
10. Efficient engraftment of genetically modified cells is necessary to ameliorate central nervous system involvement of murine model of mucopolysaccharidosis type II by hematopoietic stem cell targeted gene therapy
11. Clinical findings of gadolinium-enhanced cardiac magnetic resonance in Fabry patients
12. Fabry Disease
13. Prevention of early liver metastasis after pancreatectomy by perioperative administration of a nuclear factor-κB inhibitor in mice
14. Forced expression of DYRK2 exerts anti-tumor effects via apoptotic induction in liver cancer
15. The beneficial effects of long-term enzyme replacement therapy on cardiac involvement in Japanese Fabry patients
16. Efficacy and safety of migalastat in a Japanese population: a subgroup analysis of the ATTRACT study
17. Mutation spectrum of α-Galactosidase gene in Japanese patients with Fabry disease
18. Chaperone effect of sulfated disaccharide from heparin on mutant iduronate-2-sulfatase in mucopolysaccharidosis type II
19. Human Mesenchymal Stem Cells in Rodent Whole-Embryo Culture Are Reprogrammed to Contribute to Kidney Tissues
20. Recombinant thrombomodulin suppresses tumor growth of pancreatic cancer by blocking thrombin-induced PAR1 and NF-κB activation
21. Anti-BlyS antibody reduces the immune reaction against enzyme and enhances the efficacy of enzyme replacement therapy in Fabry disease model mice
22. Identification of Cryptic Novel α-Galactosidase A Gene Mutations: Abnormal mRNA Splicing and Large Deletions
23. Gene therapy for lysosomal storage diseases and peroxisomal diseases
24. Adenovirus-Mediated Gene Transfer and Expression of Human β -glucuronidase Gene in the Liver, Spleen, and Central Nervous System in Mucopolysaccharidosis Type VII Mice
25. Non-myeloablative preconditioning with ACK2 (anti-c-kit antibody) is efficient in bone marrow transplantation for murine models of mucopolysaccharidosis type II
26. New treatment strategy with nuclear factor-κB inhibitor for pancreatic cancer
27. Characteristics of Cerebral Microbleeds in Patients with Fabry Disease
28. Proteasome Inhibitor Bortezomib Enhances the Activity of Multiple Mutant Forms of Lysosomal α-Glucosidase in Pompe Disease
29. A method for measuring disease-specific iduronic acid from the non-reducing end of glycosaminoglycan in mucopolysaccharidosis type II mice
30. Dual inhibition of nuclear factor kappa-B and Mdm2 enhance the antitumor effect of radiation therapy for pancreatic cancer
31. TFEB overexpression promotes glycogen clearance of Pompe disease iPSC-derived skeletal muscle
32. Lentiviral Gene Transfer to iPS Cells: Toward the Cardiomyocyte Differentiation of Pompe Disease-Specific iPS Cells
33. Preoperative platelet to lymphocyte ratio predicts outcome of patients with pancreatic ductal adenocarcinoma after pancreatic resection
34. An awareness survey on COVID-19 among Japanese patients with Fabry disease (Short Communication)
35. Disease modeling and lentiviral gene transfer in patient-specific induced pluripotent stem cells from late-onset Pompe disease patient
36. イデンシ チリョウ ノ ゲンジョウ ト リンリテキ ショモンダイ
37. Foot Process Effacement with Normal Urinalysis in Classic Fabry Disease
38. Systemic accumulation of undigested lysosomal metabolites in an autopsy case of mucolipidosis type II; autophagic dysfunction in cardiomyocyte
39. The generation of induced pluripotent stem cells (iPSCs) from patients with infantile and late-onset types of Pompe disease and the effects of treatment with acid-α-glucosidase in Pompe's iPSCs
40. A practical fluorometric assay method to measure lysosomal acid lipase activity in dried blood spots for the screening of cholesteryl ester storage disease and Wolman disease
41. Enzyme augmentation therapy enhances the therapeutic efficacy of bone marrow transplantation in mucopolysaccharidosis type II mice
42. Inhibition of nuclear factor-κB enhances the antitumor effect of tumor necrosis factor-α gene therapy for hepatocellular carcinoma in mice
43. Combination chemotherapy of nafamostat mesylate with gemcitabine for gallbladder cancer targeting nuclear factor-κB activation
44. Morphological features of iPS cells generated from Fabry disease skin fibroblasts using Sendai virus vector (SeVdp)
45. Combination chemotherapy of serine protease inhibitor nafamostat mesilate with oxaliplatin targeting NF-κB activation for pancreatic cancer
46. Novel interferon-based pre-transplantation conditioning in the treatment of a congenital metabolic disorder
47. Inhibition of Nuclear Factor Kappa-B Enhances the Antitumor Effect of Combination Treatment with Tumor Necrosis Factor-Alpha Gene Therapy and Gemcitabine for Pancreatic Cancer in Mice
48. No accumulation of globotriaosylceramide in the heart of a patient with the E66Q mutation in the α-galactosidase A gene
49. Akt inactivation induces endoplasmic reticulum stress-independent autophagy in fibroblasts from patients with Pompe disease
50. Long-term efficacy of hematopoietic stem cell transplantation on brain involvement in patients with mucopolysaccharidosis type II: A nationwide survey in Japan
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