312 results on '"Spinal muscular atrophy -- Care and treatment"'
Search Results
2. Early Life Safety Profiling of Gene Therapy for Spinal Muscular Atrophy: A Case Series Analysis
3. Children's Hospital of Fudan University Researchers Highlight Research in Spinal Muscular Atrophy (Safety analysis of laboratory parameters in paediatric patients with spinal muscular atrophy treated with nusinersen)
4. TOWIE star furiously reveals her terminally ill sister was kicked out of kids' disco due to condition; Former The Only Way Is Essex star Kelsey Stratford has hit out at an organisation for the way they treated he 12-year-old sister, who has spinal muscular atrophy type 1
5. Innovative treatment gives hope for a full life to spinal muscular atrophy patients
6. Researcher at Institute of Mother and Child Has Published New Data on Spinal Muscular Atrophy (The First Patient in Poland Treated for SMA with Nusinersen During Pregnancy)
7. Research from D.O. Ott Research Institute of Obstetrics Provides New Data on Spinal Muscular Atrophy (The Relevance of Spinal Muscular Atrophy Biomarkers in the Treatment Era)
8. Mosaic to create foundation for spinal muscular atrophy
9. Reports from Stanford University Medical Center Advance Knowledge in Gene Therapy (Adeno-associated Virus Serotype 9 Antibody Seroprevalence for Patients In the United States With Spinal Muscular Atrophy)
10. Patient-specific responses to SMN2 splice-modifying treatments in spinal muscular atrophy fibroblasts
11. EU Contract Notice: Kliniczny Szpital Wojewodzki nr 2 im. sw. Jadwigi Krolowej w Rzeszowie Issues contract notice|solicitation for 'Purchase and delivery of medicines for patients qualified for the drug program - Treatment of patients with cystic fibrosis B.112 and the drug Onasemnogen Abeparvowek for the treatment of spinal muscular atrophy under the framework agreement'
12. Spinal Muscular Atrophy and Access to Rare Diseases
13. Investing in Rare Diseases: Dallas-based Taysha aims to commercialize groundbreaking gene therapies to benefit its shareholders--and desperately ill children
14. Ottawa Hospital Research Institute Researchers Have Provided New Study Findings on Gene Therapy (Expanding the Availability of Onasemnogene Abeparvovec to Older Patients: The Evolving Treatment Landscape for Spinal Muscular Atrophy)
15. Reports from University of Alberta Add New Study Findings to Research in Antisense Technology (Challenges and future perspective of antisense therapy for spinal muscular atrophy: A review)
16. Medicines For Patients With Spinal Muscular Atrophy, 2 Lots
17. Medicines For Patients With Spinal Muscular Atrophy (dk 021:2015: 33600000-6 Pharmaceutical Products, Inn: Risdiplam)
18. Studies from Yonsei University College of Medicine Further Understanding of Gene Therapy (Usefulness of YouTube in Sharing Information about New Gene Therapy for Spinal Muscular Atrophy: A Content Analysis)
19. Findings from University of Milan in the Area of Gene Therapy Described (Bridging the Gap: Gene Therapy In a Patient With Spinal Muscular Atrophy Type 1)
20. Laboratory of Translational Neuroscience Researchers Add New Study Findings to Research in Spinal Muscular Atrophy (Nusinersen Induces Disease-Severity-Specific Neurometabolic Effects in Spinal Muscular Atrophy)
21. Effect of decompressive cervical spine surgery on hypertension in patients with cervical spondylotic myelopathy - A retrospective observational study
22. Research from Institute of Biomedical Research Yields New Findings on Spinal Muscular Atrophy [Neurodegeneration Biomarkers in Adult Spinal Muscular Atrophy (SMA) Patients Treated with Nusinersen]
23. Study Results from Evelina London Children's Hospital Provide New Insights into Gene Therapy [Changes in Ventilatory Support Requirements of Spinal Muscular Atrophy (SMA) Patients Post Gene-Based Therapies]
24. Australia : Life changing gene therapy for babies with spinal muscular atrophy
25. Supplies Of A Medicinal Product In The Drug Program 'treatment Of Spinal Muscular Atrophy' - Divided Into Parts
26. Biohaven Completes Enrollment in Pivotal Phase 3 Study of Taldefgrobep Alfa in Spinal Muscular Atrophy
27. Purchase And Supply Of The Drug Nusinersen For Use In The Drug Program For The Treatment Of Spinal Muscular Atrophy Under A Framework Agreement
28. Studies from Johns Hopkins University in the Area of Gene Therapy Described (Coverage of Genetic Therapies for Spinal Muscular Atrophy Across Fee-for-service Medicaid Programs)
29. CHMP recommends Roche's Evrysdi for babies under two months old with spinal muscular atrophy (SMA)
30. New 36-Month Apitegromab Extension Data Reinforce Long-Term Substantial & Sustained Improvement of Motor Function in Phase 2 TOPAZ Trial Patients with Nonambulatory Spinal Muscular Atrophy
31. Purchase And Delivery Of The Drug Nusinersen For Use In The Drug Program For The Treatment Of Spinal Muscular Atrophy Under The Framework Agreement
32. Medical Food Products For Patients With Spinal Muscular Atrophy, 4 Lots
33. Medicines For Patients With Spinal Muscular Atrophy, 2 Lots
34. Chugai introduces Evrysdi dry syrup 60 mg to treat spinal muscular atrophy
35. SMA is no longer untreatable Speakers call for free treatment of patients suffering from spinal muscular atrophy
36. Roche launches Evrysdi to treat spinal muscular atrophy in India
37. Chugai Pharma's Evrysdi receives Japanese approval to treat spinal muscular atrophy
38. Findings from Indiana University in Spinal Muscular Atrophy Reported (The White Coat Cape: an Ethical Analysis of Emerging Therapies To Treat Spinal Muscular Atrophy)
39. Study Findings from Kitasato University Provide New Insights into Spinal Muscular Atrophy (Posterior Spinal Correction and Fusion Surgery in Patients with Spinal Muscular Atrophy-Associated Scoliosis for Whom Treatment with Nusinersen Was ...)
40. PTC Therapeutics Announces the European Approval of Evrysdi[TM] for the Treatment of Spinal Muscular Atrophy
41. CHMP Adopts Positive Opinion for Evrysdi[TM] for the Treatment of Spinal Muscular Atrophy in Adults and Children Aged Two Months and Older
42. Farmacol Logistyka Sp. z o.o., ul. Szopienicka 77, 40-431 secures contract for Purchase and delivery of Nusinersen for use in the mediocre treatment of spinal muscular atrophy under the framework agreement
43. Heartbroken Redcar family's fundraising plea and search for treatment after baby girl's devastating diagnosis; Sienna Gibson, aged just six months, has been diagnosed with Type One Spinal Muscular Atrophy
44. New treatments for spinal muscular atrophy
45. New Spinal Muscular Atrophy Study Findings Recently Were Reported by Researchers at Oregon Health & Science University (OHSU) (Nusinersen In Adult Patients With Spinal Muscular Atrophy Observations From a Single Center)
46. Nationwide Children's Hospital Details Findings in Spinal Muscular Atrophy (The Respiratory Impact of Novel Therapies for Spinal Muscular Atrophy)
47. Researchers at Shandong University Target Spinal Muscular Atrophy (Cell-Based Therapy for Spinal Muscular Atrophy)
48. PTC Therapeutics' Evrysdi receives Brazilian ANVISA approval to treat spinal muscular atrophy
49. Chugai files NDA with Japanese MHLW for risdiplam to treat spinal muscular atrophy
50. New Spinal Muscular Atrophy Findings Reported from University Hospitals Leuven (Nusinersen treatment significantly improves hand grip strength, hand motor function and MRC sum scores in adult patients with spinal muscular atrophy types 3 and 4)
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