37,356 results on '"thalassemia"'
Search Results
2. Addition of JSP191 (C-kit Antibody) to Nonmyeloablative Hematopoietic Cell Transplantation for Sickle Cell Disease and Beta-Thalassemia
3. Study of Safety & PK of Luspatercept (ACE-536) in Pediatric Participants With Beta (β)-Thalassemia
4. A Study to Evaluate Long-term Safety in Participants Who Have Participated in Other Luspatercept (ACE-536) Clinical Trials
5. A Research Study of the Effect of Food on Etavopivat in Healthy Participants
6. Detection of Krupple Like Factor -1(KLF1/ EKLF) DNA Mutations in Beta Thalassemia Patients
7. Determination of Red Cell Survival in Sickle Cell Disease and Other Hemoglobinopathies Using Biotin Labeling
8. A Study to Test the Safety, Tolerability, and Efficacy of an Antibody, REGN7999, Injected Under the Skin for the Treatment of Iron Overload in Adult Participants With Non-Transfusion Dependent β-thalassemia, Using MRI Scans to Measure Iron Levels in the Body (FERVENT-1)
9. Investigating the Mechanistic Effects of Mitapivat in Subjects With Sickle Cell Disease
10. Red Blood Cell - IMProving trAnsfusions for Chronically Transfused Recipients (RBC-IMPACT)
11. Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease
12. A Study to Determine the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of AG-348 in Adult Participants With Non-transfusion-dependent Thalassemia
13. A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT) (ENERGIZE-T)
14. A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Non-Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-NTDT) (ENERGIZE)
15. Thyroid Function , HbA1c in Relation to Ferritin Level in Adullt Patient e B Thalassemia
16. A Safety and Efficacy Study Evaluating CTX001 in Subjects With Transfusion-Dependent β-Thalassemia
17. A Study of Immune Suppression Treatment for People With Sickle Cell Disease or β-Thalassemia Who Are Going to Receive an Allogeneic Hematopoietic Cell Transplantation (HCT)
18. CS-101 in Patients With β-thalassemia
19. A Clinical Study Evaluating the Safety and Efficacy of CS-101 in Treating Subjects With β-thalassemia
20. Tissue Repository Providing Annotated Biospecimens for Approved Investigator-directed Biomedical Research Initiatives
21. Thrombophilia In Beta Thalassemia
22. ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
23. CINC424A2X01B Rollover Protocol
24. A Study to Evaluate the Safety and Effectiveness of Luspatercept for the Treatment of Transfusion-dependent (TD) Anemia Associated With Myelodysplastic Syndromes (MDS) & Beta-thalassemia (β-Thal) in India
25. A Safety and Efficacy Study Evaluating CS-101 in Subjects With β-Thalassemia Major
26. Base-edited Autologous Hematopoietic Stem Cell Transplantation in Treating Patients With β-thalassemia Major
27. PINPOINT: Gaming Technology for SCD Pain (Pinpoint II)
28. Baby Detect : Genomic Newborn Screening
29. A Study Evaluating the Safety and Efficacy of the BD211 Drug Product in β-Thalassemia Major Participants
30. Pilot Study PBSCT With TCRab Depletion For Hemoglobinopathies
31. A Study to Evaluate Luspatercept (ACE-536) in Chinese Participants Who Require Regular Red Blood Cell Transfusions Due to Beta (β)-Thalassemia.
32. At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic Conditions
33. ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia
34. A Long-Term Follow-Up Study of Participants With Sickle Cell Disease or Transfusion Dependent β-Thalassemia Who Received EDIT-301
35. A Post-Marketing Surveillance Study to Assess Safety of Luspatercept in Korean Patients With Myelodysplastic Syndrome or β-thalassemia
36. Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT)
37. A Study of Etavopivat in Patients With Thalassemia or Sickle Cell Disease
38. Collection of Human Biospecimens for Basic and Clinical Research Into Globin Variants
39. Safety & Efficacy of Thalidomide in Children With Transfusion Dependent Thalassemia
40. The BENeFiTS Trial in Beta Thalassemia Intermedia (PB04-001)
41. Fludarabine Phosphate, Cyclophosphamide, Total Body Irradiation, and Donor Stem Cell Transplant in Treating Patients With Blood Cancer
42. Early Check: Expanded Screening in Newborns
43. Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapy
44. Long-term Follow-up Study of BRL-101 for TDT
45. Study of the Role of Genetic Modifiers in Hemoglobinopathies (INHERENT)
46. Long-term Follow-up Study of BHC001 for TDT
47. Safety and Efficacy of Early Treatment With Deferiprone in Infants and Young Children (START)
48. An Open-label Study of a Gene Therapy Product in Beta-Thalassemia
49. Comparison Of Efficacy And Safety Of Thalidomide Vs Hydroxyurea In Thalassemia Patients: A Single-Centre Pilot Study.
50. A Study of Safety and Efficiency of AND017 in Patients With Transfusion Dependent and Non-transfusion Dependent β-thalassemia
Catalog
Books, media, physical & digital resources
Discovery Service for Jio Institute Digital Library
For full access to our library's resources, please sign in.