Efficacy of migalastat in a cohort of male patients with the classic Fabry phenotype in the FACETS phase 3 study.

Subjects

Subjects :

*ANGIOKERATOMA corporis diffusum
*DRUG efficacy
*LYSOSOMAL storage diseases
*MONONUCLEAR leukocytes
*GENETIC mutation

Details

Language :

English

ISSN :

10967192

Volume :

120

Issue :

1/2

Database :

Academic Search Index

Journal :

Molecular Genetics & Metabolism

Publication Type :

Academic Journal

Accession number :

121104325

Full Text :

https://doi.org/10.1016/j.ymgme.2016.11.111