Efficacy and safety of migalastat, an oral pharmacologic chaperone for Fabry disease: results from two randomized phase 3 studies, FACETS and ATTRACT.

Subjects

Subjects :

*ANGIOKERATOMA corporis diffusum
*LYSOSOMAL storage diseases
*BIOACCUMULATION
*MOLECULAR chaperones
*GENETIC mutation
*THERAPEUTICS
*PATIENTS

Details

Language :

English

ISSN :

10967192

Volume :

120

Issue :

1/2

Database :

Academic Search Index

Journal :

Molecular Genetics & Metabolism

Publication Type :

Academic Journal

Accession number :

121104606

Full Text :

https://doi.org/10.1016/j.ymgme.2016.11.093