The first study investigating safety and efficacy of velmanase alfa (human recombinant alpha mannosidase) in alpha-mannosidosis patients below six years of age.

Subjects

Subjects :

*MANNOSIDASE genetics
*LYSOSOMAL storage diseases
*MANNOSIDASES
*BODY weight
*LYMPHOCYTES

Details

Language :

English

ISSN :

10967192

Volume :

126

Issue :

2

Database :

Academic Search Index

Journal :

Molecular Genetics & Metabolism

Publication Type :

Academic Journal

Accession number :

134447884

Full Text :

https://doi.org/10.1016/j.ymgme.2018.12.153