Venglustat in adult Gaucher disease type 3: Preliminary safety, pharmacology, and exploratory efficacy from a phase 2 trial in combination with imiglucerase (LEAP).

Subjects

Subjects :

*GAUCHER'S disease
*GLUCOSYLCERAMIDES
*BIOLOGICAL tags
*PULMONARY function tests
*HEMOGLOBINS

Details

Language :

English

ISSN :

10967192

Volume :

126

Issue :

2

Database :

Academic Search Index

Journal :

Molecular Genetics & Metabolism

Publication Type :

Academic Journal

Accession number :

134448067

Full Text :

https://doi.org/10.1016/j.ymgme.2018.12.336