Survival and developmental milestones among Pompe registry patients with classic infantile-onset Pompe disease with different timing of initiation of treatment with enzyme replacement therapy (ERT).

Details

Language :

English

ISSN :

10967192

Volume :

111

Issue :

2

Database :

Academic Search Index

Journal :

Molecular Genetics & Metabolism

Publication Type :

Academic Journal

Accession number :

94076406

Full Text :

https://doi.org/10.1016/j.ymgme.2013.12.057