Efficacy of hematopoietic cell transplantation in metachromatic leukodystrophy: the Dutch experience.

Authors :: van Rappard DF
Boelens JJ
van Egmond ME
Kuball J
van Hasselt PM
Oostrom KJ
Pouwels PJ
van der Knaap MS
Hollak CE
Wolf NI
Source :: Blood [Blood] 2016 Jun 16; Vol. 127 (24), pp. 3098-101. Date of Electronic Publication: 2016 Apr 26.
Publication Year :: 2016

Subjects :: Adolescent
Adult
Child
Child, Preschool
Cognition
Cohort Studies
Humans
Leukodystrophy, Metachromatic epidemiology
Leukodystrophy, Metachromatic physiopathology
Netherlands epidemiology
Survival Analysis
Treatment Outcome
Young Adult
Hematopoietic Stem Cell Transplantation
Leukodystrophy, Metachromatic therapy

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