The Two Substrate Reduction Therapies for Type 1 Gaucher Disease Are Not Equivalent. Comment on Hughes et al. Switching between Enzyme Replacement Therapies and Substrate Reduction Therapies in Patients with Gaucher Disease: Data from the Gaucher Outcome Survey (GOS). J. Clin. Med. 2022, 11 , 5158.

Authors :: Mistry PK
Kishnani PS
Balwani M
Charrow JM
Hull J
Weinreb NJ
Cox TM
Source :: Journal of clinical medicine [J Clin Med] 2023 May 04; Vol. 12 (9). Date of Electronic Publication: 2023 May 04.
Publication Year :: 2023
Abstract: In their paper, Hughes et al. [...].

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