A Pilot Phase 2 Study with Long-Term Extension to Assess the Safety and Efficacy of Sirolimus in Patients with Leigh Syndrome Caused by Genetically-Confirmed Mitochondrial Respiratory Chain Deficiency.

Details

Language :

English

ISSN :

10860223

Database :

Supplemental Index

Journal :

Hepatitis Weekly

Publication Type :

Periodical

Accession number :

183489239