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High-Risk Population Screening for Gaucher Disease: Final Results and Key Learnings from an Italian Multicenter Observational Study

Authors :
Motta, Irene
Benedetto, Christian
Stroppiano, Marina
Cassinerio, Elena
Consonni, Dario
Borin, Lorenza
Ranalli, Paola
Barcellini, Wilma
Cappellini, Maria Domenica
Source :
Blood; November 2020, Vol. 136 Issue: Supplement 1 p17-18, 2p
Publication Year :
2020

Abstract

Motta: Sanofi Genzyme:Honoraria.Barcellini:Agios:Honoraria, Membership on an entity's Board of Directors or advisory committees, Research Funding;Novartis:Honoraria, Other: invited speaker , Research Funding;Bioverativ:Membership on an entity's Board of Directors or advisory committees;Incyte:Membership on an entity's Board of Directors or advisory committees;Alexion:Honoraria, Membership on an entity's Board of Directors or advisory committees, Other: invited speaker , Research Funding.Cappellini:BMS:Honoraria;Genzyme/Sanofi:Honoraria, Membership on an entity's Board of Directors or advisory committees;CRISPR Therapeutics, Novartis, Vifor Pharma:Membership on an entity's Board of Directors or advisory committees.

Details

Language :
English
ISSN :
00064971 and 15280020
Volume :
136
Issue :
Supplement 1
Database :
Supplemental Index
Journal :
Blood
Publication Type :
Periodical
Accession number :
ejs54555908
Full Text :
https://doi.org/10.1182/blood-2020-141527