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Childhood Langerhans cell histiocytosis hematological involvement: severity associated with BRAFV600Eloads

Authors :
Thalhammer, Julian
Jeziorski, Eric
Marec-Bérard, Perrine
Barkaoui, Mohamed Aziz
Pagnier, Anne
Rohrlich, Pierre-Simon
Chevallier, Aurore
Carausu, Liana
Aladjidi, Nathalie
Rigaud, Charlotte
Leruste, Amaury
Azarnoush, Saba
Lauvray, Thomas
Le Louet, Solenne
Gandemer, Virginie
Treguier, Pauline
Mansuy, Ludovic
Pasquet, Marlene
Olivier, Laura
Rome, Angélique
Saultier, Paul
Isfan, Fiorentina
Renard, Cécile
Li Thiao Te, Valerie
Salmon, Alexandra
Blanc, Laurence
Abou Chahla, Wadih
Lambilliotte, Anne
Stephan, Jean-Louis
Geissmann, Frederic
Lejeune, Julien
Mallebranche, Coralie
Reguerre, Yves
Grain, Audrey
Thomas, Caroline
Hélias-Rodzewicz, Zofia
Moshous, Despina
Fenneteau, Odile
Coulomb-L’Hermine, Aurore
Lapillonne, Hélène
de Saint-Basile, Geneviève
Emile, Jean-François
Héritier, Sébastien
Donadieu, Jean
Devoldere, Catherine
Gourmel, Antoine
Lutun, Anne
Leglise, Sophie
Pellier, Isabelle
Proust, Stéphanie
Cheikh, Nathalie
Klein, Sébastien
Simon, Pauline
Verite, Cécile
Miaz, Leila
Bodet, Damien
Deparis, Marianna
Gaudichon, Jérémie
Dore, Eric
Kanold, Justyna
Briandet, Claire
Desplantes, Claire
Neuman, Florent
Adjaoud, Dalila
Armari-Alla, Corinne
Plantaz, Dominique
Perret, Cécile
Bruno, Bénedicte
Nelken, Brigitte
Piguet, Christophe
Bertrand, Yves
Garnier, Nathalie
Kebaili, Kamila
Ouachee, Marie
Coze, Carole
Curtillet, Catherine
Gentet, Jean-Claude
Michel, Gérard
Galambrun, Claire
Chastagner, Pascal
Boutroux, Hélène
Landman-Parker, Judith
Bodak, Nathalie
Leverger, Guy
Petit, Arnaud
Simonin, Mathieu
Tabone, Marie-Dominique
Bader-Meunier, Brigitte
Blanche, Stéphane
Castelle, Martin
Neven, Bénédicte
Bodemer, Christine
Perrin, Olivia Boccara
Aerts, Isabelle
Orbach, Daniel
Bourdeaut, Franck
Brugieres, Laurence
Dufour, Christelle
Minard, Véronique
Valteau-Couanet, Dominique
Blanc, Laurence
Millot, Frédéric
Guimard, Grégory
Pluchart, Claire
Bonneau, Jacinthe
Chappe, Céline
Taque, Sophie
Pertuisel, Sophie
Gandemer, Virginie
Probert, Jamie
Puiseux, Chloé
Buchbinder, Nimrod
Dumesnil, Cécile
Filhon, Bruno
Marie-Cardine, Aude
Schneider, Pascale
Berger, Claire
Thouvenin-Doulet, Sandrine
Entz-Werle, Natacha
Paillard, Catherine
Spiegel, Alexandra
Plat, Geneviève
Blouin, Pascale
Jourdain, Anne
Yvert-Guillebert, Marion
Jehanne, Mathilde
Benadiba, Joy
Soler, Christine
Poiree, Maryline
Haouy, Stéphanie
Sirvent, Nicolas
Saumet, Laure
Source :
Blood; March 2025, Vol. 145 Issue: 10 p1061-1073, 13p
Publication Year :
2025

Abstract

•LCH-HI is life threatening, defined as hemoglobin ≤7 g/dL and/or platelets ≤20 × 109/L.•LCH-HI severity, associated with BRAFV600Evariant and macrophage activation, may require early MAPK inhibitors.

Details

Language :
English
ISSN :
00064971 and 15280020
Volume :
145
Issue :
10
Database :
Supplemental Index
Journal :
Blood
Publication Type :
Periodical
Accession number :
ejs67904470
Full Text :
https://doi.org/10.1182/blood.2024025625