Impact of elosulfase alfa in patients with Morquio syndrome type A who have limited ambulation: An open-label, phase 2 study

Authors :: Tarekegn Geberhiwot
Barbara K. Burton
Celeste Decker
Eugen Mengel
Kenneth I. Berger
Christian J. Hendriksz
Andrea Jester
Zlatko Sisic
Marsha Treadwell
Paul Harmatz
Source :: Molecular Genetics and Metabolism. 117:S55
Publication Year :: 2016
Publisher :: Elsevier BV, 2016.

Subjects :: Morquio syndrome
Pediatrics
medicine.medical_specialty
business.industry
Endocrinology, Diabetes and Metabolism
Phases of clinical research
medicine.disease
Biochemistry
chemistry.chemical_compound
Endocrinology
Elosulfase alfa
chemistry
Genetics
medicine
Physical therapy
In patient
Open label
business
Molecular Biology

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