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Feasibility and Safety of Systemic rAAV9-hNAGLU Delivery for Treating MPS IIIB: Toxicology, Bio-distribution and Immunological Assessments in Primates
- Source :
- Human Gene Therapy Clinical Development. :150127063140004
- Publication Year :
- 2014
- Publisher :
- Mary Ann Liebert Inc, 2014.
- Subjects :
- Toxicology
business.industry
Medicine
business
Bio distribution
Genetics (clinical)
Subjects
Details
- ISSN :
- 23248645 and 23248637
- Database :
- OpenAIRE
- Journal :
- Human Gene Therapy Clinical Development
- Accession number :
- edsair.doi...........29a94ce2ea2b9afc16d328b878908716