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Feasibility and Safety of Systemic rAAV9-hNAGLU Delivery for Treating MPS IIIB: Toxicology, Bio-distribution and Immunological Assessments in Primates

Details

ISSN :
23248645 and 23248637
Database :
OpenAIRE
Journal :
Human Gene Therapy Clinical Development
Accession number :
edsair.doi...........29a94ce2ea2b9afc16d328b878908716