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Lentiviral-mediated Gene Therapy for Adults and Children with Severe Pyruvate Kinase Deficiency: Results from an Ongoing Global Phase 1 Study
- Source :
- Blood. 140:4902-4903
- Publication Year :
- 2022
- Publisher :
- American Society of Hematology, 2022.
- Subjects :
- Immunology
Cell Biology
Hematology
Biochemistry
Subjects
Details
- ISSN :
- 15280020 and 00064971
- Volume :
- 140
- Database :
- OpenAIRE
- Journal :
- Blood
- Accession number :
- edsair.doi...........3a6d3275b2e9b38dbb643d18045e7845