Overlapping and divergent hepatic and lipoprotein phenotypes in untreated adults with acid sphingomyelinase deficiency versus untreated adults with Gaucher disease from two pivotal clinical trials

Subjects

Subjects :

Endocrinology
Endocrinology, Diabetes and Metabolism
Genetics
Molecular Biology
Biochemistry

Details

ISSN :

10967192

Volume :

135

Database :

OpenAIRE

Journal :

Molecular Genetics and Metabolism

Accession number :

edsair.doi...........4157589ebf9b97d40029bb3cd7a32de6

Full Text :

https://doi.org/10.1016/j.ymgme.2021.11.058