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PRECLINICAL DATA SUPPORTING POTENTIAL EFFICACY OF VERVE-201 - AN INVESTIGATIONAL CRISPR BASE EDITING MEDICINE TARGETING ANGPTL3 - IN PRIMARY HUMAN CELLS, MICE, AND NON-HUMAN PRIMATES

Authors :
Richard Lee
Jamie Denizio
Chaitali Dutta
Hui-Ting Hsu
Ryan Garrity
Alline Pacheco
Ellen Rohde
Hari Jayaram
Sekar Kathiresan
Andrew Bellinger
Amit V. Khera
Source :
Journal of the American College of Cardiology. 81:1115
Publication Year :
2023
Publisher :
Elsevier BV, 2023.

Details

ISSN :
07351097
Volume :
81
Database :
OpenAIRE
Journal :
Journal of the American College of Cardiology
Accession number :
edsair.doi...........439e73bf131306197f22bb1570aefea6
Full Text :
https://doi.org/10.1016/s0735-1097(23)01559-0