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O.4 Forelimb loco-regional injection of rAAV8-U7snRNA in GRMD dogs allows dose-dependant dystrophin expression and phenotypic correction

Authors :
L. Servais
C. Le Guiner
Marie Montus
J.Y. Hogrel
P. Moullier
Yan Cherel
Pierre G. Carlier
Yves Fromes
Luis Garcia
T. Voit
Source :
Neuromuscular Disorders. 21:641
Publication Year :
2011
Publisher :
Elsevier BV, 2011.

Details

ISSN :
09608966
Volume :
21
Database :
OpenAIRE
Journal :
Neuromuscular Disorders
Accession number :
edsair.doi...........4bd6546e643b19413fb9b253f6c00ae9
Full Text :
https://doi.org/10.1016/j.nmd.2011.06.760