P.69NEO1 and NEO-EXT studies: exploratory efficacy of repeat avalglucosidase alfa dosing for up to 5 years in participants with late-onset Pompe disease (LOPD)

Subjects

Subjects :

Pediatrics
medicine.medical_specialty
Neurology
business.industry
Pediatrics, Perinatology and Child Health
Medicine
Late onset
Neurology (clinical)
Dosing
Disease
business
Genetics (clinical)

Details

ISSN :

09608966

Volume :

29

Database :

OpenAIRE

Journal :

Neuromuscular Disorders

Accession number :

edsair.doi...........72f565dc4c5c312ef05b3fd8deda023f

Full Text :

https://doi.org/10.1016/j.nmd.2019.06.098