Open-label expanded access study of taliglucerase alfa in patients with Gaucher disease requiring enzyme replacement therapy

Subjects

Subjects :

Pediatrics
medicine.medical_specialty
business.industry
Endocrinology, Diabetes and Metabolism
Expanded Access Study
Disease
Enzyme replacement therapy
Biochemistry
Taliglucerase alfa
Endocrinology
Genetics
Medicine
In patient
Open label
business
Molecular Biology

Details

ISSN :

10967192

Volume :

123

Database :

OpenAIRE

Journal :

Molecular Genetics and Metabolism

Accession number :

edsair.doi...........8f4d2c3292693176d881eadaab718e6c

Full Text :

https://doi.org/10.1016/j.ymgme.2017.12.208