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P.367Comparative analysis of single stranded rAAV vectors expressing human SMN1 in correcting spinal muscular atrophy in mice

Authors :
M. Marinello
Virginie Latournerie
Samia Martin
J. Cosette
J. Denard
D. Bonnin
Anna Buj-Bello
Source :
Neuromuscular Disorders. 29:S188
Publication Year :
2019
Publisher :
Elsevier BV, 2019.

Details

ISSN :
09608966
Volume :
29
Database :
OpenAIRE
Journal :
Neuromuscular Disorders
Accession number :
edsair.doi...........a717aec90d6d62cd1f2468d9c6542189
Full Text :
https://doi.org/10.1016/j.nmd.2019.06.529