Interim Results from an Ongoing Phase 1/2 Study of Lentiviral-mediated Ex-vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I)

Authors :: Claire Booth
Julián Sevilla
Gayatri R. Rao
Maria Chitty Lopez
Elena Almarza
Dayna Terrazas
Josune Zubicaray
Marta González Vicent
Kritika Chetty
Grainne O'Toole
Jinhua Xu-Bayford
Eileen Nicoletti
Augustine Fernandes
Caroline Kuo
Satiro de Oliveira
Theodore B. Moore
Grace Choi
Miriam Zeini
Cristina Mesa-Núñez
Adrian J. Thrasher
Juan A. Bueren
Jonathan D. Schwartz
Donald B. Kohn
Source :: Blood. 140:7774-7775
Publication Year :: 2022
Publisher :: American Society of Hematology, 2022.

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