Long-term safety and efficacy of vestronidase alfa, rhGUS enzyme replacement therapy, in subjects with mucopolysaccharidosis type VII

Subjects

Subjects :

Endocrinology
Endocrinology, Diabetes and Metabolism
Genetics
Molecular Biology
Biochemistry

Details

ISSN :

10967192

Volume :

129

Database :

OpenAIRE

Journal :

Molecular Genetics and Metabolism

Accession number :

edsair.doi...........df44fb3610d6948946b5142339f1b27b

Full Text :

https://doi.org/10.1016/j.ymgme.2019.11.422