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A luciferase reporter mouse model to optimize in vivo gene editing validated by lipid nanoparticle delivery of adenine base editors
- Source :
- Molecular Therapy. 31:1159-1166
- Publication Year :
- 2023
- Publisher :
- Elsevier BV, 2023.
- Subjects :
- Pharmacology
Drug Discovery
Genetics
Molecular Medicine
Molecular Biology
Subjects
Details
- ISSN :
- 15250016
- Volume :
- 31
- Database :
- OpenAIRE
- Journal :
- Molecular Therapy
- Accession number :
- edsair.doi...........e0352ab3dd2123eb7ea046ef0234a675
- Full Text :
- https://doi.org/10.1016/j.ymthe.2023.02.009