Efficacy and safety of avalglucosidase alfa in participants with late-onset Pompe disease after 145 weeks of treatment during the COMET trial

Subjects

Subjects :

Endocrinology
Endocrinology, Diabetes and Metabolism
Genetics
Molecular Biology
Biochemistry

Details

ISSN :

10967192

Volume :

138

Database :

OpenAIRE

Journal :

Molecular Genetics and Metabolism

Accession number :

edsair.doi...........fd5a5f4858cc8cbc9651e597cf8db827

Full Text :

https://doi.org/10.1016/j.ymgme.2022.107185