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Enhancement of exon skipping in mdx52 mice by 2′-O-methyl-2-thioribothymidine incorporation into phosphorothioate oligonucleotides

Authors :
Shin'ichi Takeda
Tetsuya Nagata
Mitsuo Sekine
Takashi Kanamori
Yoshiaki Masaki
Takeshi Inde
Jun Tanihata
Kohji Seio
Source :
Med. Chem. Commun.. 6:630-633
Publication Year :
2014

Abstract

Incorporation of 2′-O-methyl-2-thioribothymidine (s2Tm) into antisense oligoribonucleotides significantly enhanced the exon skipping activity in Duchenne muscular dystrophy model mice.

Details

Language :
English
Volume :
6
Database :
OpenAIRE
Journal :
Med. Chem. Commun.
Accession number :
edsair.doi.dedup.....2cfe83afc06759685facafc3788e53b2