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Defining a new immune deficiency syndrome: MAN2B2-CDG

Authors :
Luigi D. Notarangelo
Julie E. Niemela
Kerry Dobbs
Sunnie Wong
Jan Verheijen
Gerard T. Berry
Uimook Choi
Marita Bosticardo
Miao He
Hasan Al-Dhekri
Jared H. Rowe
Lauren A. Henderson
Melissa M. Hazen
Sung-Yun Pai
Anne Marie Comeau
Sergio D. Rosenzweig
Enrica Calzoni
Erin Janssen
Eva Morava
Jennifer Stoddard
Yasuhiro Yamazaki
Kimiyo Raymond
Ottavia M. Delmonte
Source :
Journal of Allergy and Clinical Immunology, J Allergy Clin Immunol
Publication Year :
2020

Abstract

Summary We describe the first case of MAN2B2 deficiency in a patient with immune dysregulation, developmental delay, and stroke. Altered mannosylation profile was restored in patient cells upon transduction of wild-type MAN2B2.

Details

Language :
English
Database :
OpenAIRE
Journal :
Journal of Allergy and Clinical Immunology, J Allergy Clin Immunol
Accession number :
edsair.doi.dedup.....413636bad566af86f9b95141eae74c86