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Overall Health, Daily Functioning, and Quality of Life in Acute Hepatic Porphyria Patients: ENVISION, a Phase 3 Global, Multicenter, Randomized, Double-Blind, Placebo-Controlled Trial

Authors :
Eliane Sardh
Ulrich Stölzel
Gayle Ross
Daphne Vassiliou
Jerzy Windyga
Charles J. Parker
Amy Simon
Sioban Keel
Raili Kauppinen
Craig Penz
T. Lin
Janneke G. Langendonk
Yutaka Horie
Paolo Ventura
Penelope E. Stein
A. Sasapu
Bruce Ritchie
Bruce Wang
Aneta Ivanova
Laurent Gouya
Peter Stewart
John D. Phillips
Delia D'Avola
T. Nakahara
Manisha Balwani
Karl E. Anderson
D.M. Bissell
David C. Rees
P. Aguilera Peiro
Herbert L. Bonkovsky
Pauline Harper
Samuel M. Silver
Jeeyoung Oh
John J. Ko
Jiaan-Der Wang
O. Hother-Nielsen
M.J. Lee
Sushama Scalera
Source :
Sardh, E, Gouya, L, Rees, D C, Stein, P, Stoelzel, U, Aguilera Peiro, P, Bissell, D M, Bonkovsky, H L, Keel, S, Parker, C, Phillips, J D, Silver, S, Windyga, J, D'Avola, D, Ross, G, Stewart, P, Ritchie, B, Oh, J, Harper, P, Wang, J D, Langendonk, J G, Ivanova, A, Horie, Y, Anderson, K E, Ventura, P, Kauppinen, R, Vassiliou, D, Wang, B, Hother-Nielsen, O, Nakahara, T, Lee, M J, Sasapu, A, Scalera, S, Lin, T, Penz, C, Simon, A, Ko, J & Balwani, M 2020, ' Overall Health, Daily Functioning, and Quality of Life in Acute Hepatic Porphyria Patients : ENVISION, a Phase 3 Global, Multicenter, Randomized, Double-Blind, Placebo-Controlled Trial ', Digestive and Liver Disease, vol. 52, no. Suppl. 1, pp. E35 . https://doi.org/10.1016/j.dld.2019.12.123
Publication Year :
2020
Publisher :
Elsevier BV, 2020.

Details

ISSN :
15908658
Volume :
52
Database :
OpenAIRE
Journal :
Digestive and Liver Disease
Accession number :
edsair.doi.dedup.....4a3c86a09a54fd6ef507322b981490dd