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In vivo gene editing works in humans: Results of a phase 1 clinical trial for TTR amyloidosis

Authors :
Ana Rita Batista
Terence R. Flotte
Source :
Mol Ther
Publication Year :
2021
Publisher :
American Society of Gene & Cell Therapy, 2021.

Subjects

Subjects :
Pharmacology
biology
business.industry
Amyloidosis
Phases of clinical research
Bioinformatics
medicine.disease
Transthyretin
Genome editing
In vivo
Drug Discovery
Genetics
biology.protein
Commentary
Molecular Medicine
Medicine
business
Molecular Biology

Details

Language :
English
Database :
OpenAIRE
Journal :
Mol Ther
Accession number :
edsair.doi.dedup.....8065bc3c0afda6124ab0030cf542b7de

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