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Additional file 1 of N-acetyl-L-leucine for Niemann-Pick type C: a multinational double-blind randomized placebo-controlled crossover study

Authors :
Fields, T
M. Bremova, T
Billington, I
Churchill, GC
Evans, W
Fields, C
Galione, A
Kay, R
Mathieson, T
Martakis, K
Patterson, M
Platt, F
Factor, M
Strupp, M
Publication Year :
2023
Publisher :
figshare, 2023.

Abstract

Additional file 1: Supplementary Material I. Safety Parameters. Supplementary Material II. Data Collection.

Details

Database :
OpenAIRE
Accession number :
edsair.doi.dedup.....abd63cbd590725326ccacf66123bbffd
Full Text :
https://doi.org/10.6084/m9.figshare.23258859.v1