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Allogeneic hematopoietic stem cell transplant outcomes for patients with dominant negative IKZF1/IKAROS mutations

Allogeneic hematopoietic stem cell transplant outcomes for patients with dominant negative IKZF1/IKAROS mutations

Authors :
Asbjørg Stray-Pedersen
Nao Yoshida
Rebecca A. Marsh
Hye Sun Kuehn
Sergio D. Rosenzweig
Seiji Kojima
Claire Galambrun
Erinn S. Kellner
Vincent Barlogis
David Boutboul
Christa Krupski
Hans Christian Erichsen
Sylvain Latour
Immunology Service, Department of Laboratory Medicine, Clinical Center, NIH, Bethesda, Maryland
Department of Hematology and Oncology, Children's Medical Center, Japanese Red Cross Nagoya First Hospital, Nagoya
Department of Pediatrics, Nagoya University Graduate School of Medicine, Nagoya
Service d'Immunopathologie [Hôpital Saint-Louis, Paris]
Université Paris Diderot - Paris 7 (UPD7)-CHU Saint Louis [APHP]
Developpement Normal et Pathologique du Système Immunitaire
Université Paris Descartes - Paris 5 (UPD5)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Centre National de la Recherche Scientifique (CNRS)
Pédiatrie et oncologie pédiatrique [Hôpital de la Timone - APHM]
Aix Marseille Université (AMU)-Assistance Publique - Hôpitaux de Marseille (APHM)- Hôpital de la Timone [CHU - APHM] (TIMONE)
Service d'Hématologie pédiatrique, Hôpital de la Timone, Marseille
Assistance Publique - Hôpitaux de Marseille (APHM)- Hôpital de la Timone [CHU - APHM] (TIMONE)
Division of Human Genetics and Division of Immune Deficiency and Bone Marrow Transplant, Cincinnati Children's Hospital, Cincinnati
Université Paris Diderot - Paris 7 (UPD7)-Hopital Saint-Louis [AP-HP] (AP-HP)
Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)
Source :
Journal of Allergy and Clinical Immunology, Journal of Allergy and Clinical Immunology, Elsevier, 2019, 144 (1), pp.339-342. ⟨10.1016/j.jaci.2019.03.025⟩, Journal of Allergy and Clinical Immunology, 2019, 144 (1), pp.339-342. ⟨10.1016/j.jaci.2019.03.025⟩
Publication Year :
2019
Publisher :
Elsevier BV, 2019.

Abstract

International audience

Details

ISSN :
00916749
Volume :
144
Database :
OpenAIRE
Journal :
Journal of Allergy and Clinical Immunology
Accession number :
edsair.doi.dedup.....d74071a96808fb079e51a92a0c162046
Full Text :
https://doi.org/10.1016/j.jaci.2019.03.025