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A novel small molecule chaperone of rod opsin and its potential therapy for retinal degeneration

Authors :
Yuanyuan Chen
Yu Chen
Beata Jastrzebska
Marcin Golczak
Sahil Gulati
Hong Tang
William Seibel
Xiaoyu Li
Hui Jin
Yong Han
Songqi Gao
Jianye Zhang
Xujie Liu
Hossein Heidari-Torkabadi
Phoebe L. Stewart
William E. Harte
Gregory P. Tochtrop
Krzysztof Palczewski
Source :
Nature Communications, Vol 9, Iss 1, Pp 1-18 (2018)
Publication Year :
2018
Publisher :
Nature Portfolio, 2018.

Abstract

Mutations that lead to misfolding of rhodopsin can cause retinitis pigmentosa. Here, the authors carry out a high throughput screen to identify a small molecule chaperone of rod opsin, and show that it protects mouse models of retinitis pigmentosa from retinal degeneration.

Subjects

Subjects :
Science

Details

Language :
English
ISSN :
20411723
Volume :
9
Issue :
1
Database :
Directory of Open Access Journals
Journal :
Nature Communications
Publication Type :
Academic Journal
Accession number :
edsdoj.2d584c977cb4762bef27d1675ed8e92
Document Type :
article
Full Text :
https://doi.org/10.1038/s41467-018-04261-1