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One-year safety and efficacy of mitapivat in sickle cell disease:follow-up results of a phase 2, open-label study

Authors :
van Dijk, Myrthe J.
Rab, Minke A.E.
van Oirschot, Brigitte A.
Bos, Jennifer
Derichs, Cleo
Rijneveld, Anita W.
Cnossen, Marjon H.
Nur, Erfan
Biemond, Bart J.
Bartels, Marije
Jans, Judith J.M.
van Solinge, Wouter W.
Schutgens, Roger E.G.
van Wijk, Richard
van Beers, Eduard J.
van Dijk, Myrthe J.
Rab, Minke A.E.
van Oirschot, Brigitte A.
Bos, Jennifer
Derichs, Cleo
Rijneveld, Anita W.
Cnossen, Marjon H.
Nur, Erfan
Biemond, Bart J.
Bartels, Marije
Jans, Judith J.M.
van Solinge, Wouter W.
Schutgens, Roger E.G.
van Wijk, Richard
van Beers, Eduard J.
Source :
van Dijk , M J , Rab , M A E , van Oirschot , B A , Bos , J , Derichs , C , Rijneveld , A W , Cnossen , M H , Nur , E , Biemond , B J , Bartels , M , Jans , J J M , van Solinge , W W , Schutgens , R E G , van Wijk , R & van Beers , E J 2023 , ' One-year safety and efficacy of mitapivat in sickle cell disease : follow-up results of a phase 2, open-label study ' , Blood Advances , vol. 7 , no. 24 , pp. 7539-7550 .
Publication Year :
2023

Details

Database :
OAIster
Journal :
van Dijk , M J , Rab , M A E , van Oirschot , B A , Bos , J , Derichs , C , Rijneveld , A W , Cnossen , M H , Nur , E , Biemond , B J , Bartels , M , Jans , J J M , van Solinge , W W , Schutgens , R E G , van Wijk , R & van Beers , E J 2023 , ' One-year safety and efficacy of mitapivat in sickle cell disease : follow-up results of a phase 2, open-label study ' , Blood Advances , vol. 7 , no. 24 , pp. 7539-7550 .
Notes :
application/pdf, English
Publication Type :
Electronic Resource
Accession number :
edsoai.on1481683459
Document Type :
Electronic Resource