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Efficacy and Safety of Elexacaftor/Tezacaftor/Ivacaftor in Children 6 Through 11 Years of Age with Cystic Fibrosis Heterozygous for F508del and a Minimal Function Mutation: A Phase 3b, Randomized, Placebo-controlled Study

Authors :
Mall, Marcus A; https://orcid.org/0000-0002-4057-2199
Brugha, Rossa
Gartner, Silvia
Legg, Julian
Moeller, Alexander
Mondejar-Lopez, Pedro
Prais, Dario
Pressler, Tacjana
Ratjen, Felix
Reix, Philippe
Robinson, Paul D
Selvadurai, Hiran
Stehling, Florian
Ahluwalia, Neil
Arteaga-Solis, Emilio
Bruinsma, Bote G
Jennings, Mark
Moskowitz, Samuel M
Noel, Sabrina
Tian, Simon
Weinstock, Tanya G
Wu, Pan
Wainwright, Claire E; https://orcid.org/0000-0001-8389-3809
Davies, Jane C
Mall, Marcus A; https://orcid.org/0000-0002-4057-2199
Brugha, Rossa
Gartner, Silvia
Legg, Julian
Moeller, Alexander
Mondejar-Lopez, Pedro
Prais, Dario
Pressler, Tacjana
Ratjen, Felix
Reix, Philippe
Robinson, Paul D
Selvadurai, Hiran
Stehling, Florian
Ahluwalia, Neil
Arteaga-Solis, Emilio
Bruinsma, Bote G
Jennings, Mark
Moskowitz, Samuel M
Noel, Sabrina
Tian, Simon
Weinstock, Tanya G
Wu, Pan
Wainwright, Claire E; https://orcid.org/0000-0001-8389-3809
Davies, Jane C
Source :
Mall, Marcus A; Brugha, Rossa; Gartner, Silvia; Legg, Julian; Moeller, Alexander; Mondejar-Lopez, Pedro; Prais, Dario; Pressler, Tacjana; Ratjen, Felix; Reix, Philippe; Robinson, Paul D; Selvadurai, Hiran; Stehling, Florian; Ahluwalia, Neil; Arteaga-Solis, Emilio; Bruinsma, Bote G; Jennings, Mark; Moskowitz, Samuel M; Noel, Sabrina; Tian, Simon; Weinstock, Tanya G; Wu, Pan; Wainwright, Claire E; Davies, Jane C (2022). Efficacy and Safety of Elexacaftor/Tezacaftor/Ivacaftor in Children 6 Through 11 Years of Age with Cystic Fibrosis Heterozygous for F508del and a Minimal Function Mutation: A Phase 3b, Randomized, Placebo-controlled Study. American Journal of Respiratory and Critical Care Medicine, 206(11):1361-1369.
Publication Year :
2022

Details

Database :
OAIster
Journal :
Mall, Marcus A; Brugha, Rossa; Gartner, Silvia; Legg, Julian; Moeller, Alexander; Mondejar-Lopez, Pedro; Prais, Dario; Pressler, Tacjana; Ratjen, Felix; Reix, Philippe; Robinson, Paul D; Selvadurai, Hiran; Stehling, Florian; Ahluwalia, Neil; Arteaga-Solis, Emilio; Bruinsma, Bote G; Jennings, Mark; Moskowitz, Samuel M; Noel, Sabrina; Tian, Simon; Weinstock, Tanya G; Wu, Pan; Wainwright, Claire E; Davies, Jane C (2022). Efficacy and Safety of Elexacaftor/Tezacaftor/Ivacaftor in Children 6 Through 11 Years of Age with Cystic Fibrosis Heterozygous for F508del and a Minimal Function Mutation: A Phase 3b, Randomized, Placebo-controlled Study. American Journal of Respiratory and Critical Care Medicine, 206(11):1361-1369.
Notes :
application/pdf, info:doi/10.5167/uzh-229480, English
Publication Type :
Electronic Resource
Accession number :
edsoai.on1482455833
Document Type :
Electronic Resource